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Lysosomal Acid Lipase (LAL) Deficiency Registry
Sponsor: Alexion Pharmaceuticals, Inc.
Summary
This is an observational, multi-center, international disease registry designed to collect longitudinal data and create a knowledge base that will be utilized to improve the care and treatment of patients with LAL Deficiency. Participation in the Registry by both physicians and patients is voluntary.
Official title: An Observational Disease and Clinical Outcomes Registry of Patients With Lysosomal Acid Lipase (LAL) Deficiency
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
300
Start Date
2013-05-30
Completion Date
2029-08-30
Last Updated
2026-03-06
Healthy Volunteers
No
Conditions
Locations (104)
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Phoenix, Arizona, United States
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Stanford, California, United States
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Miramar, Florida, United States
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Orlando, Florida, United States
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Atlanta, Georgia, United States
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Chicago, Illinois, United States
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Boston, Massachusetts, United States
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Detroit, Michigan, United States
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Minneapolis, Minnesota, United States
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Jackson, Mississippi, United States
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Hackensack, NJ, 7601, New Jersey, United States
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New York, New York, United States
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The Bronx, New York, United States
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Philadelphia, Pennsylvania, United States
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Philadelphia, Pennsylvania, United States
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Philadelphia, Pennsylvania, United States
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Houston, Texas, United States
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Houston, Texas, United States
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Snyder, Texas, United States
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Tacoma, Washington, United States
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New Lambton Heights, New South Wales, Australia
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Ghent, East Flanders, Belgium
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Campinas, São Paulo, Brazil
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São Paulo, Brazil
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São Paulo, Brazil
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Sofia, Sofia-Grad, Bulgaria
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Edmonton, Alberta, Canada
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Halifax, Nova Scotia, Canada
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London, Ontario, Canada
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Québec, Canada
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Zagreb, Croatia
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Prague, Central Bohemia, Czechia
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Olomouc, Czechia
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Bron, Auvergne-Rhône-Alpes, France
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Clermont-Ferrand, Auvergne-Rhône-Alpes, France
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Clermont-Ferrand, Auvergne-Rhône-Alpes, France
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Grenoble, Auvergne-Rhône-Alpes, France
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Caen, Normandy, France
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La Rochelle, Nouvelle-Aquitaine, France
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Niort, Nouvelle-Aquitaine, France
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Nancy, Vandœuvre-lès-Nancy, France
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Dijon, France
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Nantes, France
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Paris, Île-de-France Region, France
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Munich, Bavaria, Germany
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Essen, North Rhine-Westphalia, Germany
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Mainz, Rhineland-Palatinate, Germany
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Berlin, Germany
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Athens, Attica, Greece
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Ioannina, Epirus, Greece
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Thessaloniki, Macedonia, Greece
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Dublin, Leinster, Ireland
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Petah Tikva, Central District, Israel
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Haifa, Israel
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Jerusalem, Israel
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Jerusalem, Israel
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Bari, Apulia, Italy
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Naples, Campania, Italy
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Udine, Friuli Venezia Giulia, Italy
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Genoa, Liguria, Italy
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Bergamo, Lombardy, Italy
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Milan, Lombardy, Italy
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Turin, Piedmont, Italy
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Florence, Tuscany, Italy
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Padova, Veneto, Italy
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Zapopan, Jalisco, Mexico
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Aguascalientes, Mexico
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Mexico City, Mexico
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Amsterdam, North Holland, Netherlands
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Amsterdam, North Holland, Netherlands
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Guimarães, Braga District, Portugal
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Lisbon, Portugal
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Petersburg, Leningradskaya Oblast', Russia
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Moscow, Moscow Oblast, Russia
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Moscow, Moscow Oblast, Russia
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Moscow, Moscow Oblast, Russia
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Moscow, Moscow Oblast, Russia
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Nizhny Novgorod, Nizhny Novgorod Oblast, Russia
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Riyadh, Saudi Arabia
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Riyadh, Saudi Arabia
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Ljubljana, Slovenia
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Santiago de Compostela, A Coruña, Spain
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Barakaldo, Biscay, Spain
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Logroño, La Rioja, Spain
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Burela de Cabo, Lugo, Spain
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Málaga, Málaga, Spain
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Oviedo, Principality of Asturias, Spain
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Reus, Tarragona, Spain
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A Coruña, Spain
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Albacete, Spain
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Alicante, Spain
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Barcelona, Spain
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Barcelona, Spain
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Las Palmas, Spain
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Madrid, Spain
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Madrid, Spain
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Murcia, Spain
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Valladolid, Spain
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Zaragoza, Spain
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Cambridge, Cambridgeshire, United Kingdom
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London, Greater London, United Kingdom
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Manchester, Greater Manchester, United Kingdom
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Salford, Greater Manchester, United Kingdom
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Birmingham, West Midlands, United Kingdom