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Apotransferrin in Atransferrinemia
Sponsor: Prothya Biosolutions
Summary
Atransferrinemia is a very rare disorder, which is caused by a deficiency of the protein transferrin. No regular treatment is available for these patients. The objective of this study is to investigate the pharmacokinetics, efficacy and safety of Apotransferrin replacement therapy in atransferrinemia patients.
Official title: Dose Escalating Study to Evaluate Pharmacokinetics, Efficacy and Safety of Apotransferrin in Atransferrinemia Patients
Key Details
Gender
All
Age Range
Any - Any
Study Type
INTERVENTIONAL
Enrollment
5
Start Date
2010-12
Completion Date
2028-01
Last Updated
2025-08-03
Healthy Volunteers
No
Conditions
Interventions
Human apotransferrin
intravenous infusion
Locations (3)
Klinikum Aschaffenburg
Aschaffenburg, Germany
AO San Gerardo
Monza, Italy
Vall d'Hebron Hospital
Barcelona, Spain