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RECRUITING
NCT01873924
Clinical and Neuropsychological Investigations in Batten Disease
Sponsor: University of Rochester
View on ClinicalTrials.gov
Summary
This study aims to assess the natural history of Batten disease (Neuronal Ceroid Lipofuscinosis) by obtaining information about the motor, behavioral, and functional capabilities of individuals with Batten disease. This study will also refine and validate the Unified Batten Disease Rating Scale (UBDRS) as a clinical rating instrument for Batten disease.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
500
Start Date
2004-08
Completion Date
2035-08
Last Updated
2025-09-12
Healthy Volunteers
No
Conditions
Neuronal Ceroid LipofuscinosisNeuronal Ceroid Lipofuscinosis CLN1Neuronal Ceroid Lipofuscinosis CLN2Neuronal Ceroid Lipofuscinosis CLN3Neuronal Ceroid Lipofuscinosis CLN5Neuronal Ceroid Lipofuscinosis CLN6Neuronal Ceroid Lipofuscinosis CLN7Neuronal Ceroid Lipofuscinosis CLN8Neuronal Ceroid Lipofuscinosis CLN10Batten Disease
Locations (1)
University of Rochester
Rochester, New York, United States