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The Myelin Disorders Biorepository Project
Sponsor: Children's Hospital of Philadelphia
Summary
The Myelin Disorders Biorepository Project (MDBP) seeks to collect and analyze clinical data and biological samples from leukodystrophy patients worldwide to support ongoing and future research projects. The MDBP is one of the world's largest leukodystrophy biorepositories, having enrolled nearly 2,000 affected individuals since it was launched over a decade ago. Researchers working in the biorepository hope to use these materials to uncover new genetic etiologies for various leukodystrophies, develop biomarkers for use in future clinical trials, and better understand the natural history of these disorders. The knowledge gained from these efforts may help improve the diagnostic tools and treatment options available to patients in the future.
Official title: The Myelin Disorders Biorepository Project and Global Leukodystrophy Initiative Clinical Trials Network
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
12000
Start Date
2016-12-08
Completion Date
2030-12-08
Last Updated
2025-10-23
Healthy Volunteers
No
Conditions
Locations (23)
Children's Hospital of Los Angeles
Los Angeles, California, United States
Children's Hospital of Orange County
Orange, California, United States
Stanford University (Lucile Packard Children's Hospital)
Palo Alto, California, United States
University of California, Davis (UC Davis Health)
Sacramento, California, United States
University of California, San Diego (Rady Children's Hospital)
San Diego, California, United States
UCSF Benioff Children's Hospital
San Francisco, California, United States
Children's National Medical Center
Washington D.C., District of Columbia, United States
Emory University (Children's Healthcare of Atlanta)
Atlanta, Georgia, United States
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States
Kennedy Krieger Institute
Baltimore, Maryland, United States
Massachusetts General Hospital (MGH)
Boston, Massachusetts, United States
University of Minnesota
Minneapolis, Minnesota, United States
Mayo Clinic
Rochester, Minnesota, United States
Atrium Health Wake Forest Baptist
Winston-Salem, North Carolina, United States
Akron Children's Hospital
Akron, Ohio, United States
Nationwide Children's Hospital
Columbus, Ohio, United States
The Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
University of Pennsylvania
Philadelphia, Pennsylvania, United States
University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, United States
Baylor College of Medicine (Texas Children's Hospital)
Houston, Texas, United States
UT Health Houston
Houston, Texas, United States
University of Utah (Primary Children's Hospital)
Salt Lake City, Utah, United States
Seattle Children's Hospital
Seattle, Washington, United States