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FA Clinical Outcome Measures
Sponsor: Friedreich's Ataxia Research Alliance
Summary
This multicenter natural history study aims to expand the network of clinical research centers in FA, and to provide a framework for facilitating therapeutic interventions. In addition, this study will lead to the development of valid yet sensitive clinical measures crucial to outcome assessment of patients with Friedreich's Ataxia. This study will support genetic modifier studies, biomarker studies, and frataxin protein level assessments by building a sample repository. This natural history study is no longer recruiting under this protocol NCT03090789 but remains actively recruiting under the harmonized study (UNIFAI) NCT06016946.
Official title: Clinical Outcome Measures in Friedreich's Ataxia
Key Details
Gender
All
Age Range
4 Years - 80 Years
Study Type
OBSERVATIONAL
Enrollment
2000
Start Date
2001-01-01
Completion Date
2030-01-01
Last Updated
2024-10-04
Healthy Volunteers
Yes
Locations (14)
UCLA Ataxia Center
Los Angeles, California, United States
University of Colorado
Denver, Colorado, United States
University of Florida - Neurology
Gainesville, Florida, United States
USF Ataxia Research Center
Tampa, Florida, United States
Emory University Hospital - Neurology
Atlanta, Georgia, United States
University of Iowa, Stead Family Children's Hospital
Iowa City, Iowa, United States
Ohio State University - Neurology
Columbus, Ohio, United States
Children's Hospital of Philadelphia - Neurology
Philadelphia, Pennsylvania, United States
St. Jude Children's Research Hospital
Memphis, Tennessee, United States
Murdoch Childrens Research Institute
Parkville, Victoria, Australia
The Hospital for Sick Children
Toronto, Ontario, Canada
CHUM - Hopital Notre-Dame
Montreal, Quebec, Canada
All India Institute of Medical Sciences (Aiims)
New Delhi, India
Auckland City Hospital
Auckland, New Zealand