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Longitudinal Study of Neurodegenerative Disorders
Sponsor: University of Pittsburgh
Summary
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
1500
Start Date
2012-01-11
Completion Date
2035-01
Last Updated
2026-02-09
Healthy Volunteers
No
Conditions
Interventions
Palliative Care
Collecting information about the natural progression of these diseases
Hematopoetic Stem Cell Transplantation
Following patients who have received HSCT as part of their clinical care.
Locations (1)
UPMC Children's Hospital of Pittsburgh
Pittsburgh, Pennsylvania, United States