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X-linked Hypophosphatemia Disease Monitoring Program
Sponsor: Ultragenyx Pharmaceutical Inc
Summary
The objectives of this observational study are to characterize XLH disease presentation and progression and to assess long-term effectiveness and safety of burosumab.
Official title: X-linked Hypophosphatemia Disease Monitoring Program (XLH-DMP)
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
782
Start Date
2018-07-16
Completion Date
2032-12
Last Updated
2026-02-17
Healthy Volunteers
No
Interventions
No intervention
Access to any treatment is through authorized commercial use and not as a part of this DMP
Locations (38)
Children's Hospital of Alabama
Birmingham, Alabama, United States
Children's Hospital Los Angeles
Los Angeles, California, United States
Rady Children's Hospital San Diego
San Diego, California, United States
University of California San Francisco
San Francisco, California, United States
Children's Hospital of Colorado
Aurora, Colorado, United States
Yale University School of Medicine
New Haven, Connecticut, United States
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States
Indiana University School of Medicine
Indianapolis, Indiana, United States
Johns Hopkins University
Baltimore, Maryland, United States
Boston Children's Hospital
Boston, Massachusetts, United States
Washington University School of Medicine
St Louis, Missouri, United States
Duke University
Durham, North Carolina, United States
Cincinnati Children's Hospital
Cincinnati, Ohio, United States
Nationwide Children's Hospital
Columbus, Ohio, United States
The Ohio State University Wexner Medical Center
Columbus, Ohio, United States
Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
Vanderbilt University - Department of Medicine
Nashville, Tennessee, United States
Vanderbilt University - Department of Pediatrics
Nashville, Tennessee, United States
Houston Methodist Research Institute
Houston, Texas, United States
University of Texas, Health Science Center
Houston, Texas, United States
University of Virgina School of Medicine
Charlottesville, Virginia, United States
Children's Hospital of The King's Daughter
Norfolk, Virginia, United States
Seattle Children's Hospital
Seattle, Washington, United States
American Family Children's Hospital
Madison, Wisconsin, United States
Hospital General de Niños Pedro de Elizalde
Buenos Aires, Buenos Aires F.D., Argentina
Hospital de Niños Dr. Ricardo Gutierrez
Buenos Aires, Argentina
Hospital Privado Universitario de Córdoba
Córdoba, Argentina
Hospital Universitário Alcides Carneiro (HUAC)
São José, Campina Grande - PB, Brazil
Instituto de Medicina Avancada (IMA Brasil)
São Paulo, São Paulo, Brazil
CETI - Centro de Estudos em Terapias Inovadoras
Curitiba, Brazil
Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo
São Paulo, Brazil
British Columbia Children's Hospital
Vancouver, British Columbia, Canada
Bone Research and Education Centre
Oakville, Ontario, Canada
Shiner's Hospital for Children - Canada
Montreal, Quebec, Canada
Children's Hospital Eastern Ontario Research Institute
Ottawa, Canada
Pontificia Universidad Católica de Chile
Santiago, Santiago Metropolitan, Chile
Hospital Universitario de San Vicente Fundación
Medellín, Antioquia, Colombia
Hospital Infantil Universitario de San José
Bogotá, Cundinamarca, Colombia