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Natural History Study of Patients With Canavan Disease (CANinform Study)
Sponsor: Aspa Therapeutics
Summary
This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural history of Canavan disease in children.
Official title: A Combination Retrospective Medical History and Prospective Observational Study of Patients With Canavan Disease for Assessment of Natural History of Canavan Disease
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
70
Start Date
2019-10-10
Completion Date
2025-07-31
Last Updated
2025-06-22
Healthy Volunteers
No
Conditions
Locations (3)
UCSF Benioff Children's Hospital Oakland
Oakland, California, United States
Massachusetts General Hospital
Boston, Massachusetts, United States
University Medical Center Hamburg-Eppendorf
Hamburg, Germany