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Angelman Syndrome Natural History Study
Sponsor: Boston Children's Hospital
Summary
The goal of this study is to conduct a prospective, longitudinal natural history study of children and adults with Angelman Syndrome using investigator-observed and parent-reported outcome measures to obtain data that will be useful for future clinical trials.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
300
Start Date
2018-08-01
Completion Date
2031-04
Last Updated
2025-04-03
Healthy Volunteers
No
Conditions
Locations (11)
Cedars-Sinai Guerin Children's
Los Angeles, California, United States
Rady Children's Hospital, San Diego
San Diego, California, United States
Children's Hospital Colorado, Anschutz Medical Campus
Aurora, Colorado, United States
Emory University School of Medicine
Atlanta, Georgia, United States
Rush University Children's Hospital
Chicago, Illinois, United States
Boston Children's Hospital
Boston, Massachusetts, United States
The Carolina Institute for Developmental Disabilities
Carrboro, North Carolina, United States
Monroe Carell Jr. Children's Hospital at Vanderbilt
Nashville, Tennessee, United States
Alberta Children's Hospital
Calgary, Alberta, Canada
BC Children's Hospital
Vancouver, British Columbia, Canada
Children's Hospital of Eastern Ontario
Ottawa, Ontario, Canada