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COMPLETED
NCT04630145
PHASE2/PHASE3

A Study of Bedaquiline Administered as Part of a Treatment Regimen With Clarithromycin and Ethambutol in Adult Patients With Treatment-refractory Mycobacterium Avium Complex-lung Disease (MAC-LD)

Sponsor: Janssen Pharmaceutical K.K.

View on ClinicalTrials.gov

Summary

The purpose of the study is to evaluate the efficacy of bedaquiline (BDQ) compared with rifamycin when administered as part of a treatment regimen with clarithromycin (CAM) and ethambutol (EB) in adult participants with treatment-refractory Mycobacterium avium complex-lung disease (MAC-LD) at Week 24 for microbiological assessment in mycobacteria growth indicator tube (MGIT).

Official title: A Phase 2/3, Multicenter, Randomized, Open-label, Active-controlled Study to Evaluate the Efficacy and Safety of Bedaquiline Administered as Part of a Treatment Regimen With Clarithromycin and Ethambutol in Adult Patients With Treatment-refractory Mycobacterium Avium Complex-lung Disease (MAC-LD)

Key Details

Gender

All

Age Range

20 Years - 79 Years

Study Type

INTERVENTIONAL

Enrollment

129

Start Date

2021-01-08

Completion Date

2025-11-14

Last Updated

2026-04-15

Healthy Volunteers

No

Interventions

DRUG

Bedaquiline

Participants will receive BDQ tablets only/

DRUG

Clarithromycin

Participants will receive CAM 400 or 500 mg twice a day.

DRUG

Ethambutol

Participants will receive 500 to 750 mg daily (maximum daily dose of 1.0 gram \[g\]) or 15 mg/kg once a day.

DRUG

Rifampicin

Participants will receive daily dose is 450 mg (maximum 600 mg) RFP capsule once a day.

DRUG

Rifabutin

Participants will receive daily dose of RBT 300 mg or 150 mg capsules once a day.

Locations (55)

Fukuoka University Chikushi Hospital

Chikushino-shi, Japan

St. Luke's International Hospital

Chūōku, Japan

Fukui Prefectural Hospital

Fukui-shi, Japan

National Hospital Organization Ibarakihigashi

Funaishikawa, Japan

Gifu Prefectural General Medical Center

Gifu, Japan

Hamamatsu Rosai Hospital

Hamamatsu, Japan

Seirei Hamamatsu General Hospital

Hamamatsu, Japan

National Hospital Organization Tenryu Hospital

Hamamatue, Japan

Matsunami General Hospital

Hashima-gun, Japan

Matsunami Health Promotion Clinic

Hashimagun Kasamatsucho, Japan

National Hospital Organization Himeji Medical Center

Himeji, Japan

Saitama Medical University Hospital

Iruma-gun, Japan

National Hospital Organization Minami Kyoto Hospital

Jōyō, Japan

Fukujuji Hospital

Kiyose, Japan

Kobe City Medical Center West Hospital

Kobe Nagata-Ku, Japan

National Hospital Organization Kochi National Hospital

Kochi, Japan

National Hospital Organization Fukuoka Higashi Medical Center

Koga, Japan

Saitama Prefectural Cardiovascular and Respiratory Center

Kumagaya, Japan

Rakuwakai Otowa Hospital

Kyoto, Japan

National Hospital Organization Kyoto Medical Center

Kyoto, Japan

Matsusaka Municipal Hospital

Matsusaka, Japan

Musashino Red Cross Hospital

Musashino, Japan

Nagaoka Red Cross Hospital

Nagaoka, Japan

Nagasaki University Hospital

Nagasaki, Japan

Kojunkai Daido Clinic

Nagoya, Japan

National Hospital Organization Nagoya Medical Center

Nagoya, Japan

National Hospital Organization Nishiniigata Chuo Hospital

Niigata, Japan

National Hospital Organization Omuta Hospital

Omuta, Japan

National Hospital Organization Sagamihara National Hospital

Sagamihara, Japan

Saitama City Hospital

Saitama-shi, Japan

Kinki-chuo Chest Medical Center

Sakai, Japan

Hokkaido Medical Center

Sapporo Nishi-Ku, Japan

Tohoku Medical And Pharmaceutical University Hospital

Sendai, Japan

National Hospital Organization Nara Medical Center

Shichijō, Japan

Tokyo Shinagawa Hospital

Shinagawa-ku, Japan

National Center for Global Health and Medicine

Shinjuku, Japan

Keio University Hospital

Shinjuku-ku, Japan

Nagano Prefectural Shinshu Medical Center

Suzaka, Japan

National Hospital Organization Tokyo Medical Center

Tokyo, Japan

National Hospital Organization Tokyo National Hospital

Tokyo, Japan

National Hospital Organization Osaka Toneyama Medical Center

Toyonaka-shi, Japan

Toyota Kosei Hospital

Toyota, Japan

Toyota Memorial Hospital

Toyota-shi, Japan

National Hospital Organization Ehime Medical Center

Tōon, Japan

JRC Wakayama Medical Center

Wakayama, Japan

Shimonoseki City Hospital

Yamaguchi, Japan

Kanagawa Cardiovascular And Respiratory Center

Yokohama, Japan

Chonnam National University Hospital

Gwangju, South Korea

The Catholic University of Korea, Incheon St. Mary's Hospital

Incheon, South Korea

Asan Medical Center

Seoul, South Korea

Samsung Medical Center

Seoul, South Korea

Kaohsiung Medical University Chung Ho Memorial Hospital

Kaohsiung City, Taiwan

Taichung Veterans General Hospital

Taichung, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Taipei Veterans General Hospital

Taipei, Taiwan