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Modulate-CF: Cystic Fibrosis Transmembrane Regulator (CFTR) Biomarker Study to Evaluate the Rescue of Mutant CFTR in Patients With Cystic Fibrosis Treated With CFTR-modulators
Sponsor: Charite University, Berlin, Germany
Summary
This observational study evaluates the effect of therapy with cystic fibrosis transmembrane regulator (CFTR) modulators on CFTR function measured by the CFTR biomarker intestinal current measurement (ICM), nasal potential difference (NPD) and sweat chloride in a post-approval setting in patients with cystic fibrosis (CF).
Official title: CFTR Biomarker Studie Bei Patient*Innen Mit Mukoviszidose Und CFTR-Modulatortherapie
Key Details
Gender
All
Age Range
6 Months - Any
Study Type
OBSERVATIONAL
Enrollment
500
Start Date
2018-07-01
Completion Date
2027-12-31
Last Updated
2026-02-24
Healthy Volunteers
No
Conditions
Interventions
Treatment with cystic fibrosis transmembrane regulator (CFTR) modualtors Ivacaftor, Lumacaftor-Ivacaftor, Tezacaftor-Ivacaftor, Elexacaftor-Tezacaftor-Ivacaftor, Vanzacaftor-Tezacaftor-Deutivacaftor
observational
Locations (4)
Charité - Universitätsmedizin Berlin
Berlin, State of Berlin, Germany
Justus-Liebig-University Giessen
Giessen, Germany
Hannover Medical School
Hanover, Germany
University of Heidelberg
Heidelberg, Germany