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An Open-Label Extension Study of STK-001 for Patients With Dravet Syndrome
Sponsor: Stoke Therapeutics, Inc
Summary
Stoke Therapeutics is evaluating the long-term safety \& tolerability of repeated doses of zorevunersen (STK-001) in patients with Dravet syndrome who previously participated in studies of zorevunersen. Change in seizure frequency and overall clinical status, and quality of life will be measured as secondary endpoints in this open-label study.
Official title: An Open-Label Extension Study for Patients With Dravet Syndrome Who Previously Participated in Studies of STK-001
Key Details
Gender
All
Age Range
30 Months - Any
Study Type
INTERVENTIONAL
Enrollment
60
Start Date
2021-01-20
Completion Date
2029-03-31
Last Updated
2026-02-04
Healthy Volunteers
No
Conditions
Interventions
zorevunersen (STK-001)
zorevunersen drug product is an antisense oligonucleotide administered as an intrathecal injection.
Locations (17)
University of California San Francisco Medical Center
San Francisco, California, United States
Children's Hospital Colorado
Aurora, Colorado, United States
Children's National Medical Center
Washington D.C., District of Columbia, United States
Nicklaus Children's Hospital
Miami, Florida, United States
Florida Hospital for Children
Orlando, Florida, United States
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States
University of Iowa Children's Hospital
Iowa City, Iowa, United States
Massachusetts General Hospital
Boston, Massachusetts, United States
Michigan Medicine
Ann Arbor, Michigan, United States
Mayo Clinic
Rochester, Minnesota, United States
NYU Comprehensive Epilepsy Center
New York, New York, United States
Oregon Health & Science University
Portland, Oregon, United States
Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
UT LeBonheur Pediatric Specialists, Inc.
Memphis, Tennessee, United States
Cook Children's Medical Center
Fort Worth, Texas, United States
Seattle Children's Hospital
Seattle, Washington, United States
MultiCare Health System Institute for Research and Innovation
Tacoma, Washington, United States