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ACTIVE NOT RECRUITING
NCT04740476
PHASE2

An Open-Label Extension Study of STK-001 for Patients With Dravet Syndrome

Sponsor: Stoke Therapeutics, Inc

View on ClinicalTrials.gov

Summary

Stoke Therapeutics is evaluating the long-term safety \& tolerability of repeated doses of zorevunersen (STK-001) in patients with Dravet syndrome who previously participated in studies of zorevunersen. Change in seizure frequency and overall clinical status, and quality of life will be measured as secondary endpoints in this open-label study.

Official title: An Open-Label Extension Study for Patients With Dravet Syndrome Who Previously Participated in Studies of STK-001

Key Details

Gender

All

Age Range

30 Months - Any

Study Type

INTERVENTIONAL

Enrollment

60

Start Date

2021-01-20

Completion Date

2029-03-31

Last Updated

2026-02-04

Healthy Volunteers

No

Conditions

Interventions

DRUG

zorevunersen (STK-001)

zorevunersen drug product is an antisense oligonucleotide administered as an intrathecal injection.

Locations (17)

University of California San Francisco Medical Center

San Francisco, California, United States

Children's Hospital Colorado

Aurora, Colorado, United States

Children's National Medical Center

Washington D.C., District of Columbia, United States

Nicklaus Children's Hospital

Miami, Florida, United States

Florida Hospital for Children

Orlando, Florida, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

University of Iowa Children's Hospital

Iowa City, Iowa, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Michigan Medicine

Ann Arbor, Michigan, United States

Mayo Clinic

Rochester, Minnesota, United States

NYU Comprehensive Epilepsy Center

New York, New York, United States

Oregon Health & Science University

Portland, Oregon, United States

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

UT LeBonheur Pediatric Specialists, Inc.

Memphis, Tennessee, United States

Cook Children's Medical Center

Fort Worth, Texas, United States

Seattle Children's Hospital

Seattle, Washington, United States

MultiCare Health System Institute for Research and Innovation

Tacoma, Washington, United States