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COMPLETED
NCT04770545
PHASE3

An Extension Study to Evaluate the Long-term Safety and Efficacy of Pegcetacoplan (APL-2) in Subjects With Geographic Atrophy Secondary to AMD

Sponsor: Apellis Pharmaceuticals, Inc.

View on ClinicalTrials.gov

Summary

This is a phase 3, open-label, multicenter, extension study to evaluate the long-term safety and efficacy of pegcetacoplan (APL-2) in subjects with geographic atrophy (GA) secondary to age-related macular degeneration (AMD) who participated in Study APL2-103 (NCT03777332) or completed the treatment at Month 24 of either Study APL2-303 (Derby, NCT03525613) or Study APL2-304 (Oaks, NCT03525600).

Official title: A Phase 3, Open-Label, Multicenter, Extension Study to Evaluate the Long-Term Safety and Efficacy of Pegcetacoplan in Subjects With Geographic Atrophy Secondary to Age-Related Macular Degeneration

Key Details

Gender

All

Age Range

60 Years - Any

Study Type

INTERVENTIONAL

Enrollment

792

Start Date

2021-03-04

Completion Date

2025-09-05

Last Updated

2026-06-18

Healthy Volunteers

No

Interventions

DRUG

PEGCETACOPLAN (APL-2)

Complement (C3) Inhibitor

Locations (175)

Retinal Research Institue, LLC

Phoenix, Arizona, United States

Associated Retina Consultants, Ltd.

Phoenix, Arizona, United States

California Retina Consultants

Bakersfield, California, United States

Retinal Diagnostic Center

Campbell, California, United States

The Retina Partners

Encino, California, United States

Retina Consultants of Orange County

Fullerton, California, United States

Atlantis Eyecare

Huntington Beach, California, United States

Jacobs Retina Center, UCSD

La Jolla, California, United States

Doheny Eye Center UCLA

Los Angeles, California, United States

Northern California Retina Vitreous Associates

Mountain View, California, United States

Retina Institute of California Medical Group

Palm Desert, California, United States

Byers Eye Institute, Stanford University

Palo Alto, California, United States

Retina Consultants San Diego

Poway, California, United States

Orange County Retina Medical Group

Santa Ana, California, United States

California Retina Consultants

Santa Barbara, California, United States

Bay Area Retina Associates

Walnut Creek, California, United States

Southwest Retina Research Center, LLC

Durango, Colorado, United States

Danbury Eye Physicians & Surgeons, PC

Danbury, Connecticut, United States

Retina Group of New England - New London

Waterford, Connecticut, United States

Florida Eye Microsurgical Institute, Inc.

Boynton Beach, Florida, United States

Blue Ocean Clinical Research

Clearwater, Florida, United States

Pinnacle Research Insitute

Fort Lauderdale, Florida, United States

Retina Health Center

Fort Myers, Florida, United States

National Opthalmic Research Institute

Fort Myers, Florida, United States

Bascom Palmer Eye Institute

Miami, Florida, United States

Bascom Palmer Eye Institute at Naples

Naples, Florida, United States

Palm Beach Gardens

Palm Beach Gardens, Florida, United States

Retina Specialty Institute

Pensacola, Florida, United States

Eye Associates of Pinellas

Pinellas Park, Florida, United States

East Florida Eye Institute

Stuart, Florida, United States

Retina Associates of Florida

Tampa, Florida, United States

University of South Florida

Tampa, Florida, United States

Center for Retina and Macular Disease

Winter Haven, Florida, United States

Southeast Retina Center, PC

Augusta, Georgia, United States

Georgia Retina, PC

Marietta, Georgia, United States

Gailey Eye Clinic Retina Center

Bloomington, Illinois, United States

Northwestern Feinberg School of Medicine

Chicago, Illinois, United States

Rush University Medical Center

Chicago, Illinois, United States

Midwest Eye Institute

Indianapolis, Indiana, United States

Retina and Vitreous Associates of Kentucky, PSC dba Retina Associates of Kentucky

Lexington, Kentucky, United States

The Retina Care Center

Baltimore, Maryland, United States

Elman Retina Group

Baltimore, Maryland, United States

The Retina Group of Washington

Chevy Chase, Maryland, United States

Cumberland Valley Retina Center

Hagerstown, Maryland, United States

Mid Atlantic Retina Specialist

Hagerstown, Maryland, United States

Ophthalmic Consultants of Boston

Boston, Massachusetts, United States

Tufts Medical Center

Boston, Massachusetts, United States

New England Retina Consultants, PC

Springfield, Massachusetts, United States

Michigan Medicine Kellogg Eye Center

Ann Arbor, Michigan, United States

Associated Retinal Consultants, PC

Grand Rapids, Michigan, United States

Associated Retinal Consultants, PC

Traverse City, Michigan, United States

Vitreoretinal Surgery

Minneapolis, Minnesota, United States

Sierra Eye Associates

Reno, Nevada, United States

Retina Center of NJ, LLC

Bloomfield, New Jersey, United States

NJ Retina

Teaneck, New Jersey, United States

NJ Retina

Toms River, New Jersey, United States

Vision Research Center Eye Associates of NM

Albuquerque, New Mexico, United States

Long Island Vitreoretinal Consultants

Great Neck, New York, United States

Vitreous Retina Macula Consultants of New York

New York, New York, United States

Ophthalmic Consultants of Long Island

Oceanside, New York, United States

Western Carolina Retinal Associates

Asheville, North Carolina, United States

Charlotte Eye Ear Nose and Throat Associates, PS

Charlotte, North Carolina, United States

Duke University, Duke Eye Center

Durham, North Carolina, United States

Graystone Eye

Hickory, North Carolina, United States

Retina Associates of Cleveland, Inc.

Cleveland, Ohio, United States

Retina Associates of Cleveland

Cleveland, Ohio, United States

Cleveland Clinic Cole Eye Institute

Cleveland, Ohio, United States

The Ohio State University

Columbus, Ohio, United States

Retina Associates of Cleveland, Inc.

Youngstown, Ohio, United States

Retina Vitreous Center, PLLC

Edmond, Oklahoma, United States

Oregon Retina LLP

Eugene, Oregon, United States

Retina Northwest, PC

Portland, Oregon, United States

Eye Health Northwest

Portland, Oregon, United States

Mid Atlantic Retina

Bethlehem, Pennsylvania, United States

Retina Vitreous Consultants

Monroeville, Pennsylvania, United States

Mid Atlantic Retina

Philadelphia, Pennsylvania, United States

Mid Atlantic Retina

Philadelphia, Pennsylvania, United States

AIO Visionary Eye Care

West Mifflin, Pennsylvania, United States

Black Hills Regional Eye Institute

Rapid City, South Dakota, United States

Charles Retina Institute

Germantown, Tennessee, United States

Tennessee Retina, PC

Nashville, Tennessee, United States

Retina Research Center PLLC

Austin, Texas, United States

Brown Retina Institute

Bellaire, Texas, United States

Texas Retina Associates

Dallas, Texas, United States

Houston Eye Associates

Houston, Texas, United States

Retina Consultants of Houston, PA

Houston, Texas, United States

Valley Retina Institute

McAllen, Texas, United States

Medical Center Ophthalmology Associates

San Antonio, Texas, United States

Retina Associates of South Texas

San Antonio, Texas, United States

Retina Consultants of Houston

The Woodlands, Texas, United States

Retina Associates of Utah, PC

Murray, Utah, United States

University of Utah - John A. Moran Center

Salt Lake City, Utah, United States

University of Virginia

Charlottesville, Virginia, United States

The Retina Group of Washington

Fairfax, Virginia, United States

Emerson Clinical Research Institute

Falls Church, Virginia, United States

Vitreoretinal Associates of Washington

Bellevue, Washington, United States

Spokane Eye Clinical Research

Spokane, Washington, United States

Retina Health Center

Madison, Wisconsin, United States

Retina-Vitreous Associates Medical Group

Madison, Wisconsin, United States

Diagnostico Ocular

Buenos Aires, Argentina

Organizacion Medica de Investigacion (OMI)

Buenos Aires, Argentina

Fundacion Zambrano

Buenos Aires, Argentina

Centro Oftalmologico Dr. Charles S.A.

Buenos Aires, Argentina

Instituto Oftalmologico de Cordoba

Córdoba, Argentina

OFTAR

Mendoza, Argentina

Microcirujia Ocular Rosario

Rosario, Argentina

Oftalmologos Especialistas

Santa Fe, Argentina

Marsden Eye Specialist

Parramatta, New South Wales, Australia

Strathfield Retina Clinic

Strathfield, New South Wales, Australia

Sydney Retina

Sydney, New South Wales, Australia

The Ashley Centre

Westmead, New South Wales, Australia

Centre for Eye Research Australia

East Melbourne, Victoria, Australia

Retina and Eye Consultantss

Hurstville, Australia

Lions Eye Institute

Nedlands, Australia

Save Sight Institute

Westmead, Australia

IPEPO Instituto Da Visao

São Paulo, Brazil

Ivey Eye Institute

London, Ontario, Canada

University of Ottawa Eye Institute

Ottawa, Ontario, Canada

Retina Centre of Ottawa

Ottawa, Ontario, Canada

Fakultni Nemocnice Ostrava

Ostrava-Poruba, Czechia

University hospital Kralovske Vinohrady

Prague, Czechia

AXON Clinical, s.r.o.

Prague, Czechia

Vseobecna fakultni nemocnice v Praze

Prague, Czechia

Gemini Eye Clinic

Zlín, Czechia

Centre ophtalmologique Saint-Exupery

Saint-Cyr-sur-Loire, Lyon, France

CHU de Bordeaux

Bordeaux, France

Centre Hospitalier Intercommunal de Creteil

Créteil, France

CHU Dijon

Dijon, France

Clinique du Val d'Ouest

Écully, France

Hopital de la Croix-Rousse

Lyon, France

Centre monticelli Paradis

Marseille, France

CHU de Nantes - Hotel Dieu

Nantes, France

Centre Ophtalmol de l Odeon

Paris, France

Hopital Lariboisiere

Paris, France

CHNO des Quinze-Vingts

Paris, France

Centre Ophtalmo. Image/Laser

Paris, France

Maison Rouge Ophthalmologic Center

Strasbourg, France

CHU de Strasbourg Hopital Civil

Strasbourg, France

Universitats-Augenklinik Bonn

Bonn, Germany

Uniklinik Koln

Cologne, Germany

University Opthalmology Clinic

Freiburg im Breisgau, Germany

Uni-medizin Gottingen Augenklinik 3.B1.261

Göttingen, Germany

Klinikum der Stadt Ludwigshafen gGmbH

Ludwigshafen, Germany

Universitatsklinikum Schleswig-Holstein

Lübeck, Germany

Augenklinik der LMU Munchen

München, Germany

Klinikum rechts der Isar

München, Germany

Augenzentrum am St. Franziskus-Hospital

Münster, Germany

Universitatsklinikum Regensburg

Münster, Germany

Universitatsklinikum Munster

Münster, Germany

STZ Eyetrial

Tübingen, Germany

Assaf ha Rofeh MC

Be’er Ya‘aqov, Israel

Rambam Health Care Campus

Haifa, Israel

Hadassah Medical Center

Jerusalem, Israel

Tel Aviv Sourasky Medical Center

Tel Aviv, Israel

IRCCS San Raffaele

Milan, Italy

ASST Fatebenefratelli-Sacco Ospedale Luigi Sacco

Milan, Italy

Academisch Medisch Centrum

Amsterdam, Netherlands

Radboud university medical center Oogheelkunde

Nijmegen, Netherlands

Southern Eye Specialists

Christchurch, New Zealand

Hamilton Eye Clinic

Hamilton, New Zealand

Eye Surgery Center Professor Zagorski

Bydgoszcz, Poland

Oftalmika Eye Hospital

Bydgoszcz, Poland

Grupo Laser Vision

Rzeszów, Poland

Oculomedica Eye Centre

Tarnów, Poland

UNO-MED Centrum Medyne

Tarnów, Poland

Hospital Universitario Puerta de Hierro

Madrid, Spain

Instituto Oftalmologico Gomez-Ulla

Santiago de Compostela, Spain

Kings College Hospital NHS Trust

London, London, United Kingdom

Huddersfield Royal Infirmary

Huddersfield, West Yorkshire, United Kingdom

St James's University Hospital

Leeds, West Yorkshire, United Kingdom

Bristol Eye Hospital

Bristol, United Kingdom

Royal Liverpool University Hospital

Liverpool, United Kingdom

London Vision Clinic

London, United Kingdom

Oxford Eye Hospital

Oxford, United Kingdom

Sunderland Eye Infirmary

Sunderland, United Kingdom