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BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)
Sponsor: Alnylam Pharmaceuticals
Summary
The purpose of this study is to describe the natural history and progression of patients diagnosed with PH1, and to characterize the long-term real-world safety and effectiveness of lumasiran.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
207
Start Date
2021-12-13
Completion Date
2028-09-01
Last Updated
2026-03-31
Healthy Volunteers
No
Conditions
Locations (30)
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Phoenix, Arizona, United States
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Washington D.C., District of Columbia, United States
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Boston, Massachusetts, United States
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Rochester, Minnesota, United States
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Cincinnati, Ohio, United States
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Pittsburgh, Pennsylvania, United States
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Dallas, Texas, United States
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Houston, Texas, United States
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Ghent, Belgium
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Liège, Belgium
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Hamilton, Ontario, Canada
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Toronto, Ontario, Canada
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Laurier, Quebec, Canada
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Bordeaux, France
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Lyon, France
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Paris, France
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Berlin, Germany
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Cologne, Germany
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Hamburg, Germany
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Jerusalem, Israel
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Orbassano, Torino, Italy
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Milan, Italy
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Verona, Italy
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Amsterdam, Netherlands
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Santa Cruz de Tenerife, Canary Islands, Spain
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Barcelona, Spain
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Las Palmas, Spain
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Bern, Switzerland
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London, England, United Kingdom
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London, United Kingdom