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A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Sponsor: ModernaTX, Inc.
Summary
The main purpose of this study is to evaluate the long-term safety of mRNA-3927 administered to participants with propionic acidemia (PA) who have previously participated in Study mRNA-3927-P101 (NCT04159103).
Official title: A Phase 1/2, Global, Open-Label, Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Key Details
Gender
All
Age Range
1 Year - Any
Study Type
INTERVENTIONAL
Enrollment
50
Start Date
2021-11-09
Completion Date
2031-12-04
Last Updated
2026-03-23
Healthy Volunteers
No
Conditions
Interventions
mRNA-3927
mRNA-3927 dispersion for IV infusion
Locations (22)
Ronald Reagan UCLA Medical Center
Los Angeles, California, United States
University of Stanford Medical Center
Palo Alto, California, United States
University of Michigan Hospitals
Ann Arbor, Michigan, United States
Icahn School of Medicine at Mount Sinai
New York, New York, United States
Duke University Medical System (Duke Health)
Durham, North Carolina, United States
The Children's Hospital of Philadelphia (CHOP)
Philadelphia, Pennsylvania, United States
Texas Children's Hospital
Houston, Texas, United States
Hospital For Sick Children
Toronto, Ontario, Canada
AP-HM- Hôpital de La Timone
Marseille, France
Hôpital Necker - Enfants Malades
Paris, France
Fujita Health University Hospital
Toyoake-shi, Akita, Japan
Tohoku University Hospital
Sendai, Miyagi, Japan
Erasmus MC -Dr. Molewaterplein 40
Rotterdam, South Holland, Netherlands
Universitair Medisch Centrum Utrecht - PPDS
Utrecht, Netherlands
King Faisal Specialist Hospital & Research Centre
Riyadh, Ar Riya, Saudi Arabia
King Abdullah Children's Specialist Hospital
Riyadh, Ar Riya, Saudi Arabia
Hospital Universitario Cruces
Barakaldo, Vizcaya, Spain
Hospital Universitario 12 de Octubre
Madrid, Spain
Willink Biochemical Genetics Unit - Manchester
Manchester, England, United Kingdom
University Hospital Birmingham NHS Foundation Trust
Birmingham, West Midlands, United Kingdom
Birmingham Women's and Children's NHS Foundation Trust
Birmingham, West Midlands, United Kingdom
Great Ormond Street Hospital for Children NHS Foundation Trust
London, United Kingdom