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A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS)
Sponsor: Ionis Pharmaceuticals, Inc.
Summary
The purpose of this study is to evaluate the effect of olezarsen (formerly known as AKCEA-APOCIII-LRx) on the percent change in fasting triglycerides (TG) from baseline.
Official title: An Open-Label Extension Study of AKCEA-APOCIII-LRx Administered Subcutaneously to Patients With Familial Chylomicronemia Syndrome (FCS)
Key Details
Gender
All
Age Range
18 Years - Any
Study Type
INTERVENTIONAL
Enrollment
60
Start Date
2021-11-18
Completion Date
2028-02
Last Updated
2025-12-12
Healthy Volunteers
No
Conditions
Interventions
Olezarsen
Olezarsen will be administered by SC injection.
Locations (27)
Diabetes/Lipid Management & Research Center
Huntington Beach, California, United States
Excel Medical Clinical Trials, LLC
Boca Raton, Florida, United States
Department of Pharmacy
Park Ridge, Illinois, United States
University of Kansas Medical Center (KUMC)
Kansas City, Kansas, United States
CTSI Investigational Pharmacy
New York, New York, United States
Milstein Hospital
New York, New York, United States
IDS Central
Philadelphia, Pennsylvania, United States
Ecogene-21
Chicoutimi, Quebec, Canada
Institute de Recherches Cliniques de Montreal
Montreal, Quebec, Canada
Nathalie Saint-Pierre
Montreal, Quebec, Canada
Clinique des Maladies Lipidiques de Quebec Inc.
Québec, Quebec, Canada
Groupement Hospitalier Est- Pharmacie Secteur Essais Clinique
Bron, France
Hôpital Bicêtre
Le Kremlin-Bicêtre, France
Pharmacie Hopital de la Conception
Marseille, France
Via Sergio Pansini 5
Naples, Italy
UOC di Farmacia AOUP PAOLO GIACCONE
Palermo, Italy
Azienda Ospedaliero Universitaria Policlinico Umberto I
Rome, Italy
Academisch Medisch Centrum Goederenontvangst Apotheek t.a.v. Kenniscentrum
Amsterdam, Noor-Holland, Netherlands
Oslo Hospital Pharmacy Rikshospitalet
Oslo, Norway
Hospital da Senhora da Oliveira Guimaraes
Creixomil, Portugal
Dra Margarida Falcao Centro Hospitalar Lisboa Ocidental Hospital Egas Moniz
Lisbon, Portugal
Metabolicke centrum MU
Bratislava, Slovakia
Hospital Clínic Barcelona C/ Villarroel
Barcelona, Spain
Hospital Universitario 12 de Octubre
Madrid, Spain
Hospital Universitario Virgen del Rocío
Seville, Spain
Apokteket AB
Malmo, Sweden
Royal Manchester Children's Hospital
Manchester, United Kingdom