Clinical Research Directory
Browse clinical research sites, groups, and studies.
Study to Evaluate the Safety and Efficacy of Daily Subcutaneous Metreleptin Treatment in Subjects With PL
Sponsor: Amryt Pharma
Summary
This is a Phase III, double-blind, placebo-controlled, safety and efficacy study of daily SC metreleptin in subjects with Partial Lipodystrophy.
Official title: A 12-Month Randomized, Multicenter, Double-Blind, Placebo-Controlled Phase 3 Study to Evaluate the Safety and Efficacy of Daily Subcutaneous Metreleptin Treatment in Subjects With Partial Lipodystrophy
Key Details
Gender
All
Age Range
12 Years - Any
Study Type
INTERVENTIONAL
Enrollment
69
Start Date
2021-12-17
Completion Date
2026-10-31
Last Updated
2025-08-29
Healthy Volunteers
No
Conditions
Interventions
metreleptin
Metreleptin is a recombinant human leptin analog that is indicated as an adjunct to diet as replacement therapy to treat the complications of leptin deficiency
Placebo
Placebo
Locations (31)
University of Alabama
Birmingham, Alabama, United States
UC Davis
Sacramento, California, United States
Flourish Boca Raton
Boca Raton, Florida, United States
Emory University
Atlanta, Georgia, United States
Massachusetts General Hospital
Boston, Massachusetts, United States
University of Michigan
Ann Arbor, Michigan, United States
Mayo Clinic
Rochester, Minnesota, United States
University of Missouri
Columbia, Missouri, United States
Amryt Research Site, Endocrinology Research Associates Inc
Columbus, Ohio, United States
The Ohio State University Wexner Medical Center
Columbus, Ohio, United States
The Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
UT Southwestern Medical Center
Dallas, Texas, United States
Medical College of Wisconsin
Milwaukee, Wisconsin, United States
UZ Leuven
Leuven, Belgium
Universitário Walter Cantídio
Fortaleza, Brazil
Insight Centro de Pesquisas
Porto Alegre, Brazil
Hospital das Clinicas FMRP-USP
Ribeirão Preto, Brazil
Instituto Estadual de Diabetes e Endocrinologia (IEDE-RJ)
Rio de Janeiro, Brazil
Nova Scotia Health
Halifax, Nova Scotia, Canada
Care Access Clinic
Sydney, Nova Scotia, Canada
Hamilton General Hospital- McMaster University
Hamilton, Ontario, Canada
London Health Science Centre
London, Ontario, Canada
Ecogene-21
Chicoutimi, Quebec, Canada
Faculty of Medicine, Universite Laval
Québec, Quebec, Canada
Universidad Catolica
Santiago, Chile
Hadassah University Hospital - Ein Kerem
Jerusalem, Israel
Leids Universitair Medisch Centrum
Leiden, Netherlands
Radboud University Medical Centre Interne Geneeskund
Nijmegen, Netherlands
Uniwersyteckie Centrum Kliniczne
Katowice, Poland
SPZOZ Szpital Uniwersytecki w Krakowie
Krakow, Poland
University Clinical Hospital of Santiago de Compostela/Hospital Universitario
Santiago de Compostela, Spain