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ADH1 and ADH2 Disease Monitoring Study (DMS)
Sponsor: Calcilytix Therapeutics, Inc., a BridgeBio company
Summary
A global, multi-center, Disease Monitoring Study (DMS) in participants with Autosomal Dominant Hypocalcemia Type 1 (ADH1) or Autosomal Dominant Hypocalcemia Type 2 (ADH2) designed to characterize ADH1 and ADH2 disease presentation and progression through retrospective (past) and longitudinal prospective (over time into the future) data collection.
Official title: Autosomal Dominant Hypocalcemia Types 1 And 2 (ADH1/2) Disease Monitoring Study (DMS)
Key Details
Gender
All
Age Range
Any - 90 Years
Study Type
OBSERVATIONAL
Enrollment
95
Start Date
2022-01-20
Completion Date
2028-12
Last Updated
2025-04-04
Healthy Volunteers
No
Conditions
Locations (27)
University of California, San Francisco (UCSF) - Benioff Children's Hospital - Oakland
Oakland, California, United States
Children's Hospital Colorado
Aurora, Colorado, United States
Nemours Children's Clinic
Jacksonville, Florida, United States
Indiana University (IU) School of Medicine - University Hospital
Indianapolis, Indiana, United States
Boston Children's Hospital
Boston, Massachusetts, United States
Mayo Clinic
Rochester, Minnesota, United States
Physician's East Endocrinology
Greenville, North Carolina, United States
Cincinnati Children's Hospital Medical Center
Cincinnati, Ohio, United States
Ohio State University Medical Center (OSUMC)
Columbus, Ohio, United States
Royal North Shore Hospital
Saint Leonards, New South Wales, Australia
Universitaire Ziekenhuizen Leuven
Leuven, Flemish Brabant, Belgium
Bone Research and Education Centre
Oakville, Ontario, Canada
Aarhus University Hospital
Aarhus, Denmark
Helsinki University Hospital (HUS) - The New Children's Hospital
Helsinki, Finland
HCL Hopital Femme Mere Enfant
Bron, Auvergne-Rhône-Alpes, France
HCL Hopital Edouard Herriot
Lyon, Auvergne-Rhône-Alpes, France
CHU de Lille
Lille, France
Departement d'Endocrinologie et Diabetes pour Enfants - AP-HP Hopital Bicetre
Le Kremlin-Bicêtre, Île-de-France Region, France
Endokrinologikum Gottingen
Göttingen, Germany
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano
Milan, Lombardy, Italy
IRCCS Ospedale San Raffaele
Milan, Lombardy, Italy
Policlinico Universitario Campus Bio-Medico
Rome, Italy
Osaka University Hospital
Osaka, Japan
The University of Tokyo Hospital
Tokyo, Japan
Erasmus MC
Rotterdam, Netherlands
Centro Hospitalar Universitario de Lisboa Norte - Hospital de Santa Maria
Lisbon, Portugal
Royal Manchester Children's Hospital
Manchester, United Kingdom