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Alpha-1 Antitrypsin Disease Cohort: Longitudinal Biomarker Study of Disease
Sponsor: Columbia University
Summary
Alpha-1 Anti-trypsin Deficiency (AATD) is a genetic disease with lung and liver disease presentations. The purpose of this study is to examine the density of the lung as measured by chest computed tomography (CT) and determine if existing emphysema predicts changes in the rate of subsequent emphysema or changes in CT, serum or plasma biomarkers of interest. The overarching goal is to develop biomarkers that can be used in interventional trials since lung function changes do not typically inform disease progression in AATD.
Official title: Alpha-1 Antitrypsin Disease Cohort: Longitudinal Biomarker Study of Disease - Alpha-1 Biomarker Research Consortium (A1BC)
Key Details
Gender
All
Age Range
18 Years - Any
Study Type
OBSERVATIONAL
Enrollment
286
Start Date
2022-03-23
Completion Date
2027-01
Last Updated
2026-01-16
Healthy Volunteers
No
Locations (9)
University of Alabama at Birmingham
Birmingham, Alabama, United States
University of California - Los Angeles
Los Angeles, California, United States
National Jewish Health
Denver, Colorado, United States
University of Chicago
Chicago, Illinois, United States
Boston University
Boston, Massachusetts, United States
Columbia University
New York, New York, United States
University of North Carolina
Chapel Hill, North Carolina, United States
Medical University of South Carolina
Charleston, South Carolina, United States
University of Utah
Salt Lake City, Utah, United States