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ENROLLING BY INVITATION
NCT05352919
PHASE3

An Extension Study to Learn More About the Long-Term Safety of Litifilimab (BIIB059) Injections and Whether They Can Improve Symptoms of Adult Participants Who Have Systemic Lupus Erythematosus

Sponsor: Biogen

View on ClinicalTrials.gov

Summary

In this study, researchers will learn more about a study drug called litifilimab (BIIB059) in participants with systemic lupus erythematosus (SLE). The study will focus on participants who have active disease and are already taking standard of care medications. These may include antimalarials, steroids, and immunosuppressants. This is an extension study of 230LE303 and 230LE304 (TOPAZ-1 and TOPAZ-2). It will enroll participants who completed the treatment periods of either one of the parent studies. The main objective of the study is to learn more about the long-term safety of litifilimab. The main question researchers want to answer is: \- How many participants have adverse events and serious adverse events? Researchers will also learn about the effect litifilimab has on controlling symptoms of SLE and lowering its activity. They will measure symptoms of SLE over time using a variety of scoring tools. These include the SLE Responder Index (SRI), the Systemic Lupus Erythematosus Disease Activity Index-2000 (SLEDAI-2K), and the British Isles Lupus Activity Group-2004 (BILAG-2004), among others. Researchers will also study how participants' immune systems respond to litifilimab. Additionally, they will measure the effect litifilimab and SLE have on the quality of life of participants using a group of questionnaires. The study will be done as follows: * The Week 52 visit of studies 230LE303 and 230LE304 will be Day 1 of this study. * Participants who were receiving either a high or low dose of litifilimab in the parent studies will continue receiving the same doses. * Participants who were receiving placebo in the parent studies will be randomized to receive either a high or low dose of litifilimab. * All participants will receive litifilimab as injections under the skin once every 4 weeks. The treatment period will last 156 weeks. Participants may continue to take their standard of care medications. * Neither the researchers nor the participants will know which doses of litifilimab the participants are receiving. * There will be a follow-up safety period that lasts up to 24 weeks. * In total, participants will have up to 47 study visits. The total study duration for participants will be up to 180 weeks. Optional Substudy: Some participants may be invited to join an optional substudy after being in the main study for at least 4 months. This substudy will test a new injector device for giving litifilimab. The injector device is an automatic device that delivers the full dose in one injection without needing to push a plunger. Researchers will compare the safety and tolerability of the injector device and how the body reacts to it to the current prefilled syringe method. The substudy will last 3 months and will include about 120 participants.

Official title: A Multicenter, Randomized, Dose-Blind, Phase 3 Long-Term Extension Study to Evaluate Continuous Safety and Efficacy of Litifilimab (BIIB059) in Adult Participants With Active Systemic Lupus Erythematosus

Key Details

Gender

All

Age Range

18 Years - Any

Study Type

INTERVENTIONAL

Enrollment

864

Start Date

2022-06-10

Completion Date

2030-03-29

Last Updated

2026-03-20

Healthy Volunteers

No

Interventions

DRUG

Litifilimab

Administered as specified in the treatment arm.

DRUG

Litifilimab-matching placebo

Administered as specified in the treatment arm.

Locations (182)

Arizona Arthritis & Rheumatology Associates, P.C.

Phoenix, Arizona, United States

Wallace Rheumatic Study Center

Beverly Hills, California, United States

Care Access Research - Huntington Beach

Huntington Beach, California, United States

Providence Facey Medical Foundation

Mission Hills, California, United States

Inland Rheumatology Clinical Trials, Inc.

Upland, California, United States

University of Colorado Denver

Aurora, Colorado, United States

Georgetown University Hospital-Medstar

Washington D.C., District of Columbia, United States

Arthritis & Rheumatic Disease Specialties

Aventura, Florida, United States

Highlands Research Institute

Avon Park, Florida, United States

Clinical Research of West Florida - Corporate

Clearwater, Florida, United States

GNP Research at Mark Jaffe, MD

Cooper City, Florida, United States

Omega Research Consultants

DeBary, Florida, United States

Life Clinical Trials

Margate, Florida, United States

Clinical Research of West Florida, Inc.

Tampa, Florida, United States

AdventHealth Medical Group

Tampa, Florida, United States

Arthritis Center of North Georgia

Gainesville, Georgia, United States

University of Massachusetts Chan Medical School

Worcester, Massachusetts, United States

AA MRC LLC Ahmed Arif Medical Research Center

Flint, Michigan, United States

Precision Comprehensive Clinical Research Solutions

Rochester Hills, Michigan, United States

Saint Louis Rheumatology

St Louis, Missouri, United States

NYU Langone Brooklyn

Brooklyn, New York, United States

DJL Clinical Research, PLLC

Charlotte, North Carolina, United States

University of Cincinnati

Cincinnati, Ohio, United States

Paramount Medical Research & Consulting, LLC

Middleburg Heights, Ohio, United States

West Tennessee Research Institute

Jackson, Tennessee, United States

Ramesh C Gupta, MD

Memphis, Tennessee, United States

Arthritis & Rheumatology Research Institute

Allen, Texas, United States

Tekton Research - PARENT

Austin, Texas, United States

Accurate Clinical Research

Baytown, Texas, United States

Precision Comprehensive Clinical Research Solution

Colleyville, Texas, United States

Precision Comprehensive Clinical Research Solutions

Colleyville, Texas, United States

Accurate Clinical Research, Inc.

Humble, Texas, United States

R and H Clinical Research

Katy, Texas, United States

Sun Research Institute, LLC

San Antonio, Texas, United States

Advanced Rheumatology of Houston

The Woodlands, Texas, United States

Swedish Medical Center

Seattle, Washington, United States

Organizacion Medica de Investigacion (OMI)

CABA, Buenos Aires, Argentina

Centro de Investigaciones Medicas Mar del Plata

Mar del Plata, Buenos Aires, Argentina

Policlìnica Red Omip S.A - Ensayos Clinicos GC

Mar del Plata, Buenos Aires, Argentina

Centro Dermatologico Schejtman

San Miguel, Buenos Aires, Argentina

Centro Medico Barrio Parque

Buenos Aires, Ciudad Autonoma Buenos Aires, Argentina

Instituto CAICI

Rosario, Santa Fe Province, Argentina

Clinica Mayo de Urgencias Medicas Cruz Blanca SRL

San Miguel de Tucumán, Tucumán Province, Argentina

Centro de Investigaciones Medicas Tucuman

San Miguel de Tucumán, Tucumán Province, Argentina

Investigaciones Clinicas Tucuman

San Miguel de Tucumán, Tucumán Province, Argentina

Hospital Italiano de La Plata

Buenos Aires, Argentina

Instituto de Investigaciones Clinicas Quilmes

Buenos Aires, Argentina

Centro Medico Dra Laura Maffei Investigacion Clinica Aplicada

Ciudad Autonoma Buenos Aires, Argentina

STAT Research S.A.

Ciudad Autonoma Buenos Aires, Argentina

Sanatorio Allende

Córdoba, Argentina

Instituto de Reumatologia

Mendoza, Argentina

CER San Juan Centro Polivalente de Asistencia e Inv. Clinica

San Juan, Argentina

Centre Hospitalier Universitaire de Liege

Liège, Belgium

HUWC - UFC - Hospital Universitário Walter Cantídio - Universidade Federal do Ceará

Fortaleza, Ceará, Brazil

CEDOES - Diagnóstico e Pesquisa

Vitória, Espírito Santo, Brazil

Clínica SER da Bahia

Salvador, Estado de Bahia, Brazil

L2IP - Instituto de Pesquisas Clínicas Ltda.

Brasília, Federal District, Brazil

IPC MT Instituto de Pesquisas Clinicas do Mato Grosso

Santo Ângelo, Mato Grosso, Brazil

Santa Casa de Misericordia de Belo Horizonte

Belo Horizonte, Minas Gerais, Brazil

CMiP - Centro Mineiro de Pesquisa

Juiz de Fora, Minas Gerais, Brazil

CETI - Centro de Estudos em Terapias Inovadoras Ltda.

Curitiba, Paraná, Brazil

Hospital de Clínicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

LMK Serviços Médicos S/S Ltda

Porto Alegre, Rio Grande do Sul, Brazil

Hospital Moinhos de Vento

Porto Alegre, Rio Grande do Sul, Brazil

Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto

Sao Jose Rio Preto, São Paulo, Brazil

Centro Multidisciplinar de Estudos Clínicos - CEMEC

São Bernardo do Campo, São Paulo, Brazil

CEPIC - Centro Paulista de Investigação Clínica e Serviços Médicos

São Paulo, São Paulo, Brazil

A2Z Clinical Centro Avancado de Pesquisa Clinica

Valinhos, São Paulo, Brazil

RDSS Ricardo Diaz Scientific Solution

São Paulo, Brazil

MC Artmed OOD

Plovdiv, Bulgaria

UMHAT "Pulmed" OOD

Plovdiv, Bulgaria

UMHAT-Plovdiv AD

Plovdiv, Bulgaria

DCC 1 - Ruse, EOOD

Rousse, Bulgaria

DCC 'Alexandrovska', EOOD

Sofia, Bulgaria

DCC Focus 5 - MEOH OOD

Sofia, Bulgaria

Military Medical Academy - MHAT - Sofia

Sofia, Bulgaria

Centro Medico Prosalud

Santiago, Chile

CTR Estudios

Santiago, Chile

Enroll Spa

Santiago, Chile

BioMedica Research Group

Santiago, Chile

Clinical Research Chile SpA.

Valdivia, Chile

Xuanwu Hospital Capital Medical University

Beijing, Beijing Municipality, China

Dongguan People's Hospital

Dongguan, Guangdong, China

Guangdong Second Provincial General Hospital

Guangzhou, Guangdong, China

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong, China

Shenzhen People's Hospital

Shenzhen, Guangdong, China

Zhongshan TCM Hospital

Zhongshan, Guangdong, China

Hainan General Hospital

Haikou, Hainan, China

The Second Hospital of Hebei Medical University

Shijiazhuang, Hebei, China

Xiangya Hospital, Central South University

Changsha, Hu'nan, China

ZhuZhou Central Hospital

Zhuzhou, Hu'nan, China

The Second Affiliated Hospital of Soochow University

Suzhou, Jiangsushe, China

Jiujiang No.1 People's Hospital

Jiujiang, Jiangxi, China

Pingxiang People's Hospital

Pingxiang, Jiangxi, China

Jilin Province People's Hospital

Changchun, Jilin, China

Binzhou Medical University Hospital

Binzhou, Shandong, China

Renji Hospital Shanghai Jiaotong University School of Medicine - West Branch

Shanghai, Shanghai Municipality, China

The First Affiliated Hospital of Ningbo University

Ningbo, Zhejiang, China

The First Hospital of Jilin University

Changchun, China

IPS Centro Medico Julian Coronel S.A.

Cali, Valle del Cauca Department, Colombia

Fundacion Cardiomet CEQUIN S.A.S

Armenia, Colombia

Centro de Investigacion Medico Asistencial S.A.S

Barranquilla, Colombia

Clínica de la Costa S.A.S

Barranquilla, Colombia

Centro de Investigacion en Reumatologia y Especialidades Medicas CIREEM S.A.S.

Bogotá, Colombia

Servimed S.A.S.

Bucaramanga, Colombia

Preventive Care Ltda

Chía, Colombia

Healthy Medical Center

Zipaquirá, Colombia

Revmatologie s.r.o.

Brno, Czechia

Fakultni nemocnice Olomouc

Olomouc, Czechia

CHU Clermont Ferrand - Hopital Gabriel Montpied

Clermont-Ferrand, Drôme, France

NNA Hospital

Athens, Attica, Greece

Vita Verum Medical Egeszsegugyi Szolgaltato Bt.

Székesfehérvár, Fejér, Hungary

Del-pesti Centrumkorhaz - Orszagos Hematologiai es Infektologiai Intezet

Budapest, Hungary

Bekes Varmegyei Kozponti Korhaz

Gyula, Hungary

Vital Medical Center

Veszprém, Hungary

Rambam Health Care Campus

Haifa, Israel

Meir Medical Center

Kfar Saba, Israel

Tel Aviv Sourasky Medical Center Pt

Tel Aviv, Israel

Azienda Ospedaliera San Camillo Forlanini

Roma, Italy

JCHO Chukyo Hospital

Nagoya, Aichi-ken, Japan

Fujita Health University Hospital

Toyoake-shi, Aichi-ken, Japan

NHO Chibahigashi National Hospital

Chiba, Chiba, Japan

KKR Hamanomachi Hospital

Fukuoka, Fukuoka, Japan

NHO Kyushu Medical Center

Fukuoka, Fukuoka, Japan

Hospital of the University of Occupational and Environmental Health

Kitakyushu-shi, Fukuoka, Japan

Hiroshima University Hospital

Hiroshima, Hiroshima, Japan

Tonan Hospital

Sapporo, Hokkaido, Japan

Japanese Red Cross Society Himeji Hospital

Himeji-shi, Hyōgo, Japan

Kobe University Hospital

Kobe, Hyōgo, Japan

Kagawa University Hospital

Kita-gun, Kagawa-ken, Japan

NHO Yokohama Medical Center

Yokohama, Kanagawa, Japan

Japanese Red Cross Kumamoto Hospital

Kumamoto, Kumamoto, Japan

Kindai University Hospital

Osakasayama-shi, Osaka, Japan

Nihon University Itabashi Hospital

Itabashi-ku, Tokyo-To, Japan

Toho University Ohashi Medical Center

Meguro-ku, Tokyo-To, Japan

Center Hospital of the National Center for Global Health and Medicine

Shinjuku-ku, Tokyo-To, Japan

Clinica de Investigacion en Reumatologia y Obesidad S.C.

Guadalajara, Jalisco, Mexico

Centro de investigacion medica y reumatologia

Guadalajara, Jalisco, Mexico

Centro de Investigacion Clínica GRAMEL S.C

Mexico City, Mexico City, Mexico

Clinstile, S.A. de C.V.

Mexico City, Mexico City, Mexico

Instituto Nacional de Ciencias Medicas y Nutricion Dr. Salvador Zubiran

Mexico City, Mexico City, Mexico

Consultorio Privado Dr. Miguel Cortes Hernandez

Cuernavaca, Morelos, Mexico

Centro Peninsular de Investigacion Clinica, SCP

Mérida, Yucatán, Mexico

Medical Care & Research SA de CV

Mérida, Yucatán, Mexico

Investigacion y Biomedicina de Chihuahua, S.C.

Chihuahua City, Mexico

Centro de Investigacion y Atencion Integral Durango CIAID

Durango, Mexico

Centro de Investigacion Clinica Inmunoreumatologia - ACQ Medic

Lima, Peru

HMA - Hospital Maria Auxiliadora

Lima, Peru

Mary Mediatrix Medical Center

Lipa City, Batangas, Philippines

Davao Doctors Hospital

Davao City, Davao Region, Philippines

University of the Philippines Manila - Philippine General Hospital

Manila, National Capital Region, Philippines

St. Luke's Medical Center

Quezon City, National Capital Region, Philippines

Far Eastern University - Dr. Nicanor Reyes Medical Foundation

Quezon City, National Capital Region, Philippines

Ospital Ng Makati

City of Taguig, Philippines

The Medical City Iloilo

Iloilo City, Philippines

Medical Center Manila

Manila, Philippines

Nova Reuma Domysławska i Rusiłowicz, Spółka Partnerska Lekarza Reumatologa i Fizjoterapeuty

Bialystok, Poland

Szpital Uniwersytecki nr 2 im.dr J. Biziela

Bydgoszcz, Poland

Nzoz Bif-Med

Bytom, Poland

Pratia MCM Krakow

Krakow, Poland

Centrum Badawcze Panaceum Agnieszka Brzezicka, Magdalena Lenkiewicz Sp. z o.o.

Malbork, Poland

Prywatna Praktyka Lekarska prof Pawel Hrycaj

Poznan, Poland

Gabinety Lekarskie Rivermed

Poznan, Poland

Przychodnia Care Access Warszawa

Warsaw, Poland

MICS Centrum Medyczne Warszawa

Warsaw, Poland

Centro Reumatologico

Caguas, Puerto Rico

S.C Centrul Medical de Diagnostic si Tratament Ambulator Neomed S.R.L

Brasov, Romania

S C Delta Health Care SRL

Bucharest, Romania

Spitalul Clinic Judetean de Urgenta Cluj Napoca

Cluj-Napoca, Romania

S.C.Centrul Medical Unirea SRL

Iași, Romania

Institute of Rheumatology

Belgrade, Serbia

University Clinical Center of Serbia

Belgrade, Serbia

Clinical Center "Bezanijska Kosa "

Belgrade, Serbia

Ajou University Hospital

Suwon, Gyeonggi-do, South Korea

Hanyang University Seoul Hospital

Seoul, South Korea

Hospital Universitario Marques de Valdecilla

Santander, Castellón, Spain

Hospital Universitario Virgen Macarena

Seville, Sevilla, Spain

Hospital Universitari Vall d'Hebron

Barcelona, Spain

Hospital Quironsalud Infanta Luisa

Seville, Spain

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, Taiwan

Guy's Hospital

London, Greater London, United Kingdom

Doncaster Royal Infirmary

Doncaster, South Yorkshire, United Kingdom