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ACTIVE NOT RECRUITING
NCT05469737
PHASE2/PHASE3

A Study to Compare the Efficacy and Safety of Oral Azacitidine Plus Best Supportive Care (BSC) Versus Placebo Plus BSC in Participants With International Prognostic Scoring System Revised (IPSS-R) Low- or Intermediate-risk Myelodysplastic Syndrome (MDS)

Sponsor: Bristol-Myers Squibb

View on ClinicalTrials.gov

Summary

The purpose of this study is to evaluate the safety and efficacy of oral azacitidine in participants with low to intermediate International Prognostic Scoring System Revised (IPSS-R) myelodysplastic syndrome (MDS).

Official title: A Phase 2/3, Multicenter, Randomized, Dose Optimization (Part I), Double-blind (Part II) Study to Compare the Efficacy and Safety of Oral Azacitidine (Oral-Aza, ONUREG®) Plus Best Supportive Care (BSC) Versus Placebo Plus BSC in Participants With IPSS-R Low- or Intermediate-risk Myelodysplastic Syndrome (MDS)

Key Details

Gender

All

Age Range

18 Years - Any

Study Type

INTERVENTIONAL

Enrollment

230

Start Date

2022-12-14

Completion Date

2028-07-31

Last Updated

2026-02-25

Healthy Volunteers

No

Interventions

DRUG

Oral Azacitidine

Specified dose on specified days

DRUG

Placebo for Oral Azacitidine

Specified dose on specified days

Locations (65)

Local Institution - 0137

Miami, Florida, United States

Local Institution - 0147

Tamarac, Florida, United States

Local Institution - 0132

East Syracuse, New York, United States

Local Institution - 0073

Pittsburgh, Pennsylvania, United States

Local Institution - 0014

Houston, Texas, United States

Local Institution - 0086

Houston, Texas, United States

Local Institution - 0123

Fairfax, Virginia, United States

Local Institution - 0070

Pilar, Buenos Aires, Argentina

Local Institution - 0039

ABB, Buenos Aires F.D., Argentina

Local Institution - 0016

Buenos Aires, Argentina

Local Institution - 0022

Buenos Aires, Argentina

Local Institution - 0050

Buenos Aires, Argentina

Local Institution - 0006

Clayton, Victoria, Australia

Local Institution - 0018

Melbourne, Victoria, Australia

Local Institution - 0004

Melbourne, Victoria, Australia

Local Institution - 0003

Melbourne, Australia

Local Institution - 0008

Toronto, Ontario, Canada

Local Institution - 0015

Toronto, Ontario, Canada

Local Institution - 0090

Montreal, Quebec, Canada

Local Institution - 0156

Wuhan, Hubei, China

Local Institution - 0060

Hradec Králové, Czechia

Local Institution - 0115

Aarhus, Central Jutland, Denmark

Local Institution - 0116

Aalborg, North Denmark, Denmark

Local Institution - 0063

Pessac, Aquitaine, France

Local Institution - 0024

Tours, Indre-et-Loire, France

Local Institution - 0094

Angers, Maine-et-Loire, France

Local Institution - 0056

Lille, Nord, France

Local Institution - 0085

Villejuif, Val-de-Marne, France

Local Institution - 0082

Paris, France

Local Institution - 0081

Duisburg, North Rhine-Westphalia, Germany

Local Institution - 0128

Düsseldorf, North Rhine-Westphalia, Germany

Local Institution - 0055

Leipzig, Saxony, Germany

Local Institution - 0037

Dresden, Germany

Local Institution - 0007

Hamburg, Germany

Local Institution - 0028

Mutlangen, Germany

Local Institution - 0125

Chaïdári, Attikí, Greece

Local Institution - 0129

Thessaloniki, Thessaloníki, Greece

Local Institution - 0127

Alexandroupoli, Greece

Local Institution - 0178

Hksar, Hong Kong

Local Institution - 0180

Shatin, Hong Kong

Local Institution - 0061

Rome, Lazio, Italy

Local Institution - 0052

Rozzano, Milano, Italy

Local Institution - 0075

Florence, Tuscany, Italy

Local Institution - 0101

Bologna, Italy

Local Institution - 0136

Kitakyushu-shi, Fukuoka, Japan

Local Institution - 0154

Sapporo, Hokkaido, Japan

Local Institution - 0153

Amagasaki, Hyōgo, Japan

Local Institution - 0130

Sagamihara, Kanagawa, Japan

Local Institution - 0135

Sendai, Miyagi, Japan

Local Institution - 0150

Shinagawa-ku, Tokyo, Japan

Local Institution - 0124

Osaka, Japan

Local Institution - 0097

Olsztyn, Warmian-Masurian Voivodeship, Poland

Local Institution - 0058

Hwasun Gun, Jeonranamdo, South Korea

Local Institution - 0048

Seoul, Seoul Teugbyeolsi, South Korea

Local Institution - 0036

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Local Institution - 0012

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Local Institution - 0051

Junggu, Taegu-Kwangyǒkshi, South Korea

Local Institution - 0109

Valencia, Valenciana, Comunitat, Spain

Local Institution - 0107

Granada, Spain

Local Institution - 0111

Madrid, Spain

Local Institution - 0112

Ourense, Spain

Local Institution - 0110

Oviedo, Spain

Local Institution - 0108

Salamanca, Spain

Local Institution - 0118

Stockholm, Stockholms Län [se-01], Sweden

Local Institution - 0119

Örebro, Örebro Län [se-18], Sweden