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Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy
Sponsor: Alexion Pharmaceuticals, Inc.
Summary
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001
Official title: A Long-term Follow-up Study of Patients in LogicBio Clinical Trials for Methylmalonic Acidemia Characterized by MMUT Mutations Who Received hLB-001
Key Details
Gender
All
Age Range
18 Years - Any
Study Type
OBSERVATIONAL
Enrollment
4
Start Date
2022-07-15
Completion Date
2037-01-01
Last Updated
2026-02-05
Healthy Volunteers
No
Conditions
Interventions
hLB-001
hLB-001 gene therapy
Locations (4)
Clinical Trial Site
Atlanta, Georgia, United States
Clinical Trial Site
Pittsburgh, Pennsylvania, United States
Clinical Trial Site
Nashville, Tennessee, United States
Clinical Trial Site
Seattle, Washington, United States