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ACTIVE NOT RECRUITING
NCT05644561
PHASE3

Evaluation of Pharmacokinetics, Pharmacodynamics, Efficacy, Safety, and Immunogenicity of Ravulizumab Administered Intravenously in Pediatric Participants With Generalized Myasthenia Gravis (gMG)

Sponsor: Alexion Pharmaceuticals, Inc.

View on ClinicalTrials.gov

Summary

The primary purpose of this study is to characterize the pharmacokinetics and pharmacodynamics of treatment with ravulizumab intravenous infusion in pediatric participants with gMG.

Official title: A Phase 3, Open-label, Single-arm, Multicenter Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Efficacy, Safety, and Immunogenicity of Ravulizumab Administered Intravenously in Pediatric Participants (6 to < 18 Years of Age) With Generalized Myasthenia Gravis (gMG)

Key Details

Gender

All

Age Range

Any - Any

Study Type

INTERVENTIONAL

Enrollment

12

Start Date

2023-06-24

Completion Date

2028-06-30

Last Updated

2026-02-19

Healthy Volunteers

No

Interventions

DRUG

Ravulizumab

Ravulizumab will be administered by intravenous (IV) infusion.

Locations (11)

Research Site

Los Angeles, California, United States

Research Site

Boston, Massachusetts, United States

Research Site

Chapel Hill, North Carolina, United States

Research Site

Philadelphia, Pennsylvania, United States

Research Site

Milan, Italy

Research Site

Roma, Italy

Research Site

Torino, Italy

Research Site

Itabashi-ku, Japan

Research Site

Belgrade, Serbia

Research Site

Belgrade, Serbia

Research Site

Bern, Switzerland