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RECRUITING
NCT05683379

AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMD

Sponsor: REGENXBIO Inc.

View on ClinicalTrials.gov

Summary

This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD).

Official title: Anti-AAV8 Antibody Assessment Study of Males With Duchenne Muscular Dystrophy Aged 0 to <25 Years

Key Details

Gender

MALE

Age Range

0 Years - 25 Years

Study Type

OBSERVATIONAL

Enrollment

200

Start Date

2022-12-20

Completion Date

2026-09

Last Updated

2025-11-25

Healthy Volunteers

No

Interventions

DIAGNOSTIC_TEST

AAV8 DetectCDx

An in vitro diagnostic assay to detect antibodies to AAV8 in human serum specimens.

Locations (1)

Rare Disease Research

Atlanta, Georgia, United States