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ENROLLING BY INVITATION
NCT05868499
PHASE1
Rollover Study From EXG-US-01
Sponsor: Elixirgen Therapeutics, Inc.
View on ClinicalTrials.gov
Summary
This is a long-term rollover follow-up study for Phase I/II study (Protocol EXG-US-01).
Official title: Long Term Follow-up Study in Patients With Telomere Biology Disorders With Bone Marrow Failure Who Completed Study EXG-US-01
Key Details
Gender
All
Age Range
18 Years - Any
Study Type
INTERVENTIONAL
Enrollment
12
Start Date
2024-01-01
Completion Date
2027-01-30
Last Updated
2024-07-12
Healthy Volunteers
No
Interventions
BIOLOGICAL
EXG34217
Single infusion
Locations (1)
Cincinnati Children's Hospital
Cincinnati, Ohio, United States