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Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Sponsor: Friedreich's Ataxia Research Alliance
Summary
This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
3000
Start Date
2023-06-28
Completion Date
2048-01-28
Last Updated
2025-06-17
Healthy Volunteers
Yes
Conditions
Locations (34)
UCLA Ataxia Center
Los Angeles, California, United States
University of Colorado
Denver, Colorado, United States
University of Florida - Neurology
Gainesville, Florida, United States
USF Ataxia Research Center
Tampa, Florida, United States
Emory University Hospital - Neurology
Atlanta, Georgia, United States
University of Iowa, Stead Family Children's Hospital
Iowa City, Iowa, United States
Ohio State University - Neurology
Columbus, Ohio, United States
Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, United States
St. Jude Children's Research Hospital
Memphis, Tennessee, United States
Murdoch Childrens Research Institute
Parkville, Victoria, Australia
Medical University Innsbruck, Department of Neurology
Innsbruck, Austria
Université Libre de Bruxelles, Hôpital Erasme, Dpt of Neurology
Brussels, Belgium
University of Campinas
Campinas, Brazil
The Hospital for Sick Children
Toronto, Ontario, Canada
CHUM - Hopital Notre-Dame
Montreal, Quebec, Canada
McGill University Health Centre - Montreal Neurological Institute
Montreal, Quebec, Canada
Motol University Hospital, Centre for Hereditary Ataxias
Prague, Czechia
Paris Brain Institute
Paris, France
Hôpital de Hautepierre, Service de Neurologie
Strasbourg, France
University Hospital Aachen, Dept. of Neurology
Aachen, Germany
Deutsches Zentrum Für Neurodegenerative Erkrankungen
Bonn, Germany
University of Munich, Dept. of Neurology, Friedrich-Baur-Institut
Munich, Germany
University of Tübingen, Dept. of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research
Tübingen, Germany
National and Kapodistrian University of Athens, Neurogenetics Unit
Athens, Greece
All India Institute of Medical Sciences (AIIMS)
New Delhi, National Capital Territory of Delhi, India
Tallaght University Hospital, Department of Neurology
Dublin, Ireland
Referente Clinico-Scientifico di Polo IRCCS "E. Medea"
Conegliano, Italy
Fondazione IRCCS Istituto Neurologico Carlo Besta
Milan, Italy
Bambino Gesù Children's Hospital, Department of Neurosciences
Roma, Italy
Stichting Radboud Universitair Medisch Centrum
Nijmegen, Netherlands
Auckland City Hospital
Auckland, New Zealand
Hospital Sant Joan de Déu, Servicio de Neurología
Barcelona, Spain
Hospital Universitario La Paz, Servicio de Neurologia
Madrid, Spain
University College of London, Ataxia Centre, National Hospital for Neurology and Neurosurgery
London, United Kingdom