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MPS (RaDiCo Cohort) (RaDiCo-MPS)
Sponsor: Institut National de la Santé Et de la Recherche Médicale, France
Summary
The goal of this observational study is to characterize the epidemiology and natural history of MPS diseases by building a retrospective and prospective collection of extensive phenotypic data from French MPS patients.
Official title: Mucopolysaccharidosis Patients in France in the Era of Specific Therapeutics
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
1000
Start Date
2017-12-20
Completion Date
2026-12
Last Updated
2026-02-11
Healthy Volunteers
No
Conditions
Locations (23)
Centre Hospitalier Universitaire d'Angers
Angers, France
Hôpital des Enfants - Groupe Hospitalier Pellegrin
Bordeaux, France
Hôpital Morvan
Brest, France
Hôpital d'Estaing
Clermont-Ferrand, France
Hôpital Beaujon
Clichy, France
Hôpital Raymond-Poincaré
Garches, France
Hôpital Jeanne de Flandre
Lille, France
Hôpital de la Timone
Marseille, France
Hôpital Gui de Chauliac
Montpellier, France
Hôpital Brabois
Nancy, France
Hôpital Armand Trousseau
Paris, France
Hôpital de la Croix Saint-Simon
Paris, France
Hôpital de la Pitié-Salpêtrière
Paris, France
Hôpital Necker-Enfants Malades
Paris, France
Hôpital Robert Debré
Paris, France
Centre Hospitalier de Pau
Pau, France
American Memorial Hospital
Reims, France
Hôpital Pontchaillou
Rennes, France
Hôpital Charles Nicolle
Rouen, France
Hôpital de Hautepierre
Strasbourg, France
Clinique Monié
Toulouse, France
Hôpital des Enfants
Toulouse, France
Hôpital Clocheville
Tours, France