Clinical Research Directory

Long Term Follow-Up for RGX-111

Sponsor: REGENXBIO Inc.

Summary

RGX-111-5101 is a long-term follow up study that evaluates the long term safety of RGX-111 in participants who have received RGX-111 (a gene therapy intended to deliver a functional copy of the alpha-L-iduronidase gene (IDUA) to the central nervous system) in a separate parent study.

Official title: A Long-term Follow-up Study to Evaluate the Safety of RGX-111

Key Details

Conditions

Interventions

Locations (2)