Clinical Research Directory
Browse clinical research sites, groups, and studies.
Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome
Sponsor: Federal Research Institute of Pediatric Hematology, Oncology and Immunology
Summary
The aim of the current study is to evaluate the safety and efficacy of low dose treosulfan based conditioning regimen in HSCT with post-transplant cyclophosphamide in Nijmegen breakage syndrome
Official title: Clinical Open-label Phase 2 Study of Low Dose Treosulfan Based Conditioning Regimen Efficacy in Hematopoietic Stem Cell Transplantation With Post-transplant Cyclophosphamide for Children Nijmegen Breakage Syndrome
Key Details
Gender
All
Age Range
3 Months - 21 Years
Study Type
INTERVENTIONAL
Enrollment
10
Start Date
2023-11-22
Completion Date
2029-01-31
Last Updated
2024-01-10
Healthy Volunteers
No
Conditions
Interventions
Treosulfan
Treosulfan 21mg/m2 (days -6, -5, -4)
Locations (1)
HSCT department
Moscow, Russia