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phenotypeS in Non Ambulant Duchenne Muscular Dystrophy
Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Summary
The aims of the study are to prospectively collect information on several aspects of function in non-ambulant DMD patients by using a structured battery of tests including motor, respiratory and cardiac function
Official title: Characterizing Phenothypes in Non Ambulant Duchenne Muscular Dystrophy
Key Details
Gender
MALE
Age Range
8 Years - 35 Years
Study Type
OBSERVATIONAL
Enrollment
250
Start Date
2022-08-30
Completion Date
2025-12-30
Last Updated
2024-10-04
Healthy Volunteers
No
Interventions
Different Phenotypes of non ambulant patients with Duchenne Muscular Dystrophy
clinical and functional data collection of non ambulant patients with Duchenne muscular dystrophy
Locations (2)
IRCCS Eugenio Medea - Ass. "La Nostra Famiglia"
Bosisio Parini, Lc, Italy
Fondazione Policlinico Universitario A. Gemelli IRCCS
Roma, Italy