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ACTIVE NOT RECRUITING
NCT06388083
PHASE2/PHASE3

A Phase 2/3 Study to Evaluate the Efficacy and Safety of Tinlarebant in Subjects With Stargardt Disease

Sponsor: Belite Bio, Inc

View on ClinicalTrials.gov

Summary

The goal of this clinical trial is to evaluate the safety, tolerability, and efficacy of tinlarebant in subjects with Stargardt Disease

Official title: A Phase 1b Open-label Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Safety, and Tolerability of Tinlarebant in Japanese Subjects With Stargardt Disease and a Phase 2/3 Randomized, Double-masked, and Placebo-controlled Study to Evaluate the Safety, Tolerability, and Efficacy of Tinlarebant in Subjects With Stargardt Disease

Key Details

Gender

All

Age Range

12 Years - 20 Years

Study Type

INTERVENTIONAL

Enrollment

60

Start Date

2024-07-31

Completion Date

2028-02

Last Updated

2026-03-12

Healthy Volunteers

No

Interventions

DRUG

Tinlarebant

5 mg tablet

DRUG

Placebo

Placebo tablets

Locations (18)

Belite Study Site - US08

Phoenix, Arizona, United States

Belite Study Site - US05

La Jolla, California, United States

Belite Study Site - US09

San Francisco, California, United States

Belite Study Site - US06

Miami, Florida, United States

Belite Study Site - US01

Boston, Massachusetts, United States

Belite Study Site - US11

Edina, Minnesota, United States

Belite Study Site - US04

Rochester, Minnesota, United States

Belite Study Site - US14

New York, New York, United States

Belite Study Site - US10

Westbury, New York, United States

Belite Study Site - US02

Durham, North Carolina, United States

Belite Study Site - US07

Philadelphia, Pennsylvania, United States

Belite Study Site - US13

Austin, Texas, United States

Belite Study Site - US03

Dallas, Texas, United States

Belite Study Site - US12

The Woodlands, Texas, United States

Belite Study Site

Kobe, Japan

Belite Study Site

Kyoto, Japan

Belite Study Site

Tokyo, Japan

UK01 Belite Study Site

London, United Kingdom