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Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
Sponsor: AstraZeneca
Summary
The MaesTTRo study aims to enroll a global cohort of patients with transthyretin (ATTR) amyloidosis to longitudinally observe the natural course of the disease and describe real-world treatment patterns and outcomes. In addition, information on the effectiveness of ATTR amyloidosis treatments, including eplontersen, which is a ligand-conjugated antisense oligonucleotide gene silencing treatment targeting activity against both the mutant and wild-type TTR protein, will be collected.
Official title: A Non-interventional, Prospective, Multi-country Study Collecting Real-world Data on the Characteristics, Treatment Patterns, and Outcomes of Patients With Transthyretin (ATTR) Amyloidosis
Key Details
Gender
All
Age Range
18 Years - 130 Years
Study Type
OBSERVATIONAL
Enrollment
1850
Start Date
2024-06-25
Completion Date
2031-12-29
Last Updated
2026-03-24
Healthy Volunteers
No
Interventions
Treatment of transthyretin (ATTR) amyloidosis in observational study setting
Data will be collected on patients with ATTR amyloidosis in a real-world setting
Locations (53)
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La Jolla, California, United States
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Los Angeles, California, United States
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San Francisco, California, United States
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San Francisco, California, United States
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New Haven, Connecticut, United States
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Washington D.C., District of Columbia, United States
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Chicago, Illinois, United States
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Indianapolis, Indiana, United States
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Boston, Massachusetts, United States
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Boston, Massachusetts, United States
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Boston, Massachusetts, United States
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Rochester, Minnesota, United States
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Kansas City, Missouri, United States
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St Louis, Missouri, United States
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New Brunswick, New Jersey, United States
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Manhasset, New York, United States
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New York, New York, United States
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New York, New York, United States
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Durham, North Carolina, United States
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Danville, Pennsylvania, United States
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Philadelphia, Pennsylvania, United States
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Philadelphia, Pennsylvania, United States
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Greenville, South Carolina, United States
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Germantown, Tennessee, United States
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Nashville, Tennessee, United States
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Dallas, Texas, United States
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Richmond, Virginia, United States
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Seattle, Washington, United States
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Milwaukee, Wisconsin, United States
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Vancouver, British Columbia, Canada
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Vancouver, British Columbia, Canada
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Halifax, Nova Scotia, Canada
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London, Ontario, Canada
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Toronto, Ontario, Canada
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Rimouski, Quebec, Canada
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Beijing, Beijing Municipality, China
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Changsha, Hunan, China
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Würzburg, Bavaria, Germany
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Frankfurt am Main, Hesse, Germany
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Hanover, Lower Saxony, Germany
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Aachen, North Rhine-Westphalia, Germany
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Cologne, North Rhine-Westphalia, Germany
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Mainz, Rhineland-Palatinate, Germany
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Homburg, Saarland, Germany
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Berlin, Germany
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Huelva, Andalusia, Spain
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Bilbao, Basque Country, Spain
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Las Palmas de Gran Canaria, Canary Islands, Spain
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Salamanca, Castille and León, Spain
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Barcelona, Catalu A, Spain
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Birmingham, West Midlands, United Kingdom
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Glasgow, United Kingdom
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London, United Kingdom