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A Long-term Follow-up Study in Participants Who Received CS-101
Sponsor: Children's Hospital of Fudan University
Summary
This is a study to evaluate the long-term safety and efficacy of CS-101 in participants who received CS-101 in study CS -101-03 (NCT06065189)
Official title: A Long-term Follow-up Study Evaluating the Safety and Efficacy of Subjects With β-thalassemia Treated With Base-edited Autologous Hematopoietic Stem Cell (CS-101) Transplantation
Key Details
Gender
All
Age Range
3 Years - 17 Years
Study Type
INTERVENTIONAL
Enrollment
5
Start Date
2024-06-18
Completion Date
2027-06
Last Updated
2025-09-10
Healthy Volunteers
No
Conditions
Interventions
CS-101
Autologous CD34+ hematopoietic stem cell suspension modified by in vitro base editing technique
Locations (1)
Children's Hospital of Fudan University
Shanghai, Shanghai Municipality, China