Clinical Research Directory

Inclusion Criteria Subjects must meet all of the following inclusion criteria for participation in this study: 1. Subject must be willing and able to provide written informed consent for the JAB-GD-001 study in accordance with applicable regulations and guidelines and to comply with all study visits and procedures. 2. Subject must have been enrolled in the preceding AVROBIO AVRO-RD-02-201 treatment study and have received AVR-RD-02 treatment Exclusion Criteria Subject has any medical, psychological, or other condition that, in the opinion of the Investigator: * Might interfere with the subject's participation in the study (including consenting to procedures); and/or * Poses any additional risk to the subject; and/or * Might confound the results of any study-required assessments.