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ACTIVE NOT RECRUITING
NCT06506084

Observational Study on the Use of Ropeginterferon Alfa-2b in Polycythemia Vera (ROPEG-PV)

Sponsor: FROM- Fondazione per la Ricerca Ospedale di Bergamo- ETS

View on ClinicalTrials.gov

Summary

Polycythaemia vera (PV) is associated with a reduced quality of life, a high rate of vascular events, and an intrinsic risk of disease evolution. The results of several randomised trials for the treatment with new cytoreductive agents are now available, among which a new ropegylated formulation of interferon alfa-2b (ropeginterferon alfa-2b) have been recently approved in Europe and USA \[EMA (2019), FDA (2021) and AIFA (2022)\]. The use of this drug in clinical practice is an opportunity for a prospective observational study in a rare disease such as PV; the aim is to evaluate its impact in the practical management of these patients. Therefore, the main objectives of the present study are to determine: (i) to what extent ropeginterferon alfa-2b can be prescribed and tolerated in patients with PV; (ii) the risk-benefit of ropeginterferon alfa-2b in patients with PV, followed-up in real-world clinical practice.

Key Details

Gender

All

Age Range

18 Years - 100 Years

Study Type

OBSERVATIONAL

Enrollment

319

Start Date

2022-09-08

Completion Date

2026-12-31

Last Updated

2025-12-26

Healthy Volunteers

Not specified

Interventions

DRUG

Ropeginterferon alfa-2b

Data will be collected at each visit during the observational study (total duration: 24 months). In accordance with routine clinical practice in this patient population, visits are expected to take place every 6 months. Patients who discontinue ropeginterferon alfa-2b treatment at any time will no longer be followed up.

Locations (37)

UOC Ematologia, ASST Papa Giovanni XXIII

Bergamo, Lombardy, Italy

Divisione Ematologia ASST, Grande Ospedale Metropolitano Niguarda

Milan, Lombardy, Italy

Divisione Ematologia, Fondazione IRCCS Policlinico San Matteo

Pavia, Lombardy, Italy

U.O. Ematologia, Ospedale di Circolo e Fondazione Macchi Varese

Varese, Lombardy, Italy

Clinica Medica I Azienda Ospedaliera di Padova

Padova, Veneto, Italy

Divisione Ematologia, Ospedale Borgo Roma

Verona, Veneto, Italy

Divisione Ematologia, Ospedale San Bortolo

Vicenza, Veneto, Italy

A.S.O. SS. Antonio e Biagio e C.Arrigo di Alessandria

Alessandria, Italy

Azienda Ospedaliera Universitaria Consorziale - Policlinico, U.O. Ematologia con Trapianto

Bari, Italy

Policlinico S. Orsola - Malpighi, Unità di Ematologia

Bologna, Italy

ASST-Spedali Civili

Brescia, Italy

Ospedale Businco, S.C. Ematologia e CTMO

Cagliari, Italy

Azienda Ospedaliero - Universitaria "Policlinico Vittorio Emanuele" - PO Gaspare Rodolico, Dipartimento di Ematologia con Trapianto di midollo Osseo

Catania, Italy

Azienda Ospedaliera S. Croce e Carle di Cuneo- Divisione di Ematologia,

Cuneo, Italy

Arcispedale Sant'Anna Azienda Ospedaliero - Universitaria di Ferrara, Unità Operativa di Ematologia

Ferrara, Italy

Azienda Ospedaliera Universitaria Careggi, Divisione di Ematologia

Florence, Italy

Azienda Ospedaliera Universitaria Policlinico "G. Martino", UOC Ematologia

Messina, Italy

Ospedale dell'Angelo, Dipartimento di Ematologia

Mestre, Italy

Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Ematologia

Milan, Italy

Ospedale San Raffaele, Unità Operativa di Ematologia e Trapianto Midollo Osseo

Milan, Italy

ASST MONZA Ospedale San Gerardo Clinica Ematologica

Monza, Italy

Azienda Ospedaliera Universitaria Federico II di Napoli Divisione di Ematologia e Trapianti del Midollo

Naples, Italy

Azienda Ospedaliero Universitaria Maggiore della Carità di Novara SCDU Ematologia

Novara, Italy

Azienda Ospedaliera Universitaria Policlinico "P. Giaccone", Divisione di Ematologia

Palermo, Italy

Azienda Ospedaliera Universitaria Pisana

Pisa, Italy

Azienda Ospedaliera San Eugenio - UOC Ematologia

Roma, Italy

Fondazione Policlinico Universitario A. Gemelli - Università Cattolica del Sacro Cuore, UCSC Ematologia

Roma, Italy

Policlinico Umberto I, Dipartimento Ematologia, Oncologia e Dermatologia

Roma, Italy

Ospedale Casa Sollievo della Sofferenza Istituto di Ricovero e Cura a Carattere Scientifico, U.O. Ematologia

San Giovanni Rotondo, Italy

A.O.U. Città della Salute e della Scienza di Torino - Ospedale Molinette- S.C. Ematologia U

Torino, Italy

Ospedale Maggiore, SC Ematologia

Trieste, Italy

Azienda Sanitaria Universitaria Integrata, Presidio Ospedaliero "Santa Maria della Misericordia", Clinica Ematologica

Udine, Italy

University Medical Center, Department of Hematology and Transplantation

Gdansk, Poland

Pratia Onkologia, Department of Hematology and Cancer Prevention

Katowice, Poland

Jagiellonian University Hospital, Department of Haematology

Krakow, Poland

Copernicus Hospital

Lodz, Poland

Medical University, Clinical Department of Haematology, Blood Neoplasms and Bone Marrow Transplantation

Wroclaw, Poland