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HAELO: A Phase 3 Study to Evaluate NTLA-2002 in Participants With Hereditary Angioedema (HAE)
Sponsor: Intellia Therapeutics
Summary
This Phase 3 study aims to evaluate the efficacy and safety of NTLA-2002 compared to placebo in participants with HAE.
Official title: HAELO: A Phase 3, Multinational, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of NTLA-2002 in Participants With Hereditary Angioedema (HAE)
Key Details
Gender
All
Age Range
16 Years - Any
Study Type
INTERVENTIONAL
Enrollment
60
Start Date
2025-01-15
Completion Date
2027-09
Last Updated
2025-12-18
Healthy Volunteers
No
Conditions
Interventions
NTLA-2002
CRISPR/Cas9 gene editing system delivered by lipid nanoparticle (LNP) for intravenous (IV) administration
Normal Saline IV Administration
The administration of intravenous (IV) normal saline
Locations (29)
Medical Research of Arizona
Scottsdale, Arizona, United States
University of California, San Diego (UCSD)
San Diego, California, United States
Raffi Tachdjian MD, Inc
Santa Monica, California, United States
Allergy & Asthma Clinical Research
Walnut Creek, California, United States
IMMUNOe International Research Centers
Centennial, Colorado, United States
Asthma & Allergy Associates
Colorado Springs, Colorado, United States
University of South Florida
Tampa, Florida, United States
Massachusetts General Hospital
Boston, Massachusetts, United States
Washington University in St. Louis
St Louis, Missouri, United States
NYU Langone Health - Long Island
Mineola, New York, United States
Icahn School of Medicine at Mount Sinai
New York, New York, United States
Bernstein Clinical Research Center, LLC
Cincinnati, Ohio, United States
Penn State Milton S. Hershey Medical Center
Hershey, Pennsylvania, United States
AARA Research Center
Dallas, Texas, United States
Campbelltown Hospital
Campbelltown, New South Wales, Australia
The Alfred Hospital
Melbourne, Victoria, Australia
Royal Melbourne Hospital
Parkville, Victoria, Australia
University of Alberta
Edmonton, Alberta, Canada
Ottawa Allergy Research Corporation
Ottawa, Ontario, Canada
CHU Grenoble-Alpes - Hopital Michallon
Grenoble, France
CHU de Lille - Hopital Claude Huriez
Lille, France
AP-HM - Hopital de la Timone
Marseille, France
Charite Universitaetsmedizin Berlin
Berlin, Germany
Universitaetsklinikum Frankfurt - Klinikum der Johann Wolfgang Goethe Universitaet
Frankfurt, Germany
Medizinische Hochschule Hannover (MHH)
Hanover, Germany
Amsterdam UMC - Locatie AMC
Amsterdam, Netherlands
New Zealand Clinical Research (NZCR)
Auckland, New Zealand
University of Cape Town - Lung Institute - Lung Clinical Research Unit
Cape Town, South Africa
Cambridge University Hospitals NHS Foundation Trust
Cambridge, United Kingdom