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A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy
Sponsor: Alnylam Pharmaceuticals
Summary
The purpose of this study is to obtain safety, efficacy, and pharmacodynamic data on the use of vutrisiran in patients with ATTR amyloidosis with cardiomyopathy who continued on extended use of vutrisiran, or switched from patisiran.
Official title: An Open-Label Extension Study to Assess the Safety and Efficacy of Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy (ATTR Amyloidosis With Cardiomyopathy)
Key Details
Gender
All
Age Range
18 Years - Any
Study Type
INTERVENTIONAL
Enrollment
700
Start Date
2024-12-03
Completion Date
2028-03-31
Last Updated
2026-02-20
Healthy Volunteers
No
Interventions
Vutrisiran
Vutrisiran administered SC q3M
Locations (87)
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Phoenix, Arizona, United States
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Beverly Hills, California, United States
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La Jolla, California, United States
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Stanford, California, United States
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Washington D.C., District of Columbia, United States
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Chicago, Illinois, United States
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Glenview, Illinois, United States
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Indianapolis, Indiana, United States
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Kansas City, Kansas, United States
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Baltimore, Maryland, United States
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Boston, Massachusetts, United States
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Boston, Massachusetts, United States
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Rochester, Minnesota, United States
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St Louis, Missouri, United States
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Omaha, Nebraska, United States
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New York, New York, United States
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New York, New York, United States
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Durham, North Carolina, United States
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Cleveland, Ohio, United States
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Columbus, Ohio, United States
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Philadelphia, Pennsylvania, United States
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Nashville, Tennessee, United States
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Dallas, Texas, United States
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Salt Lake City, Utah, United States
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Buenos Aires, Argentina
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Buenos Aires, Argentina
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Buenos Aires, Argentina
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Córdoba, Argentina
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Rosario, Argentina
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Rosario, Argentina
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Rosario, Argentina
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Vienna, Austria
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Vienna, Austria
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Aalst, Belgium
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Anderlecht, Belgium
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Dendermonde, Belgium
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Ghent, Belgium
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Hasselt, Belgium
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Leuven, Belgium
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Liège, Belgium
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Roeselare, Belgium
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Ribeirão Preto, Brazil
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Ribeirão Preto, Brazil
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Rio de Janeiro, Brazil
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São Paulo, Brazil
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São Paulo, Brazil
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Prague, Czechia
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Prague, Czechia
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Prague, Czechia
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Aarhus N, Denmark
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København Ø, Denmark
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Odense C, Denmark
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Créteil, France
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Marseille, France
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Paris, France
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Rennes, France
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Toulouse, France
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Bologna, Italy
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Florence, Italy
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Pavia, Italy
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Groningen, Netherlands
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Maastricht, Netherlands
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Utrecht, Netherlands
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Oslo, Norway
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Creixomil, Portugal
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Lisbon, Portugal
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Porto, Portugal
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Viseu, Portugal
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Seoul, South Korea
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Seoul, South Korea
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Seoul, South Korea
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Barcelona, Spain
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Bilbao, Spain
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L'Hospitalet de Llobregat, Spain
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Madrid, Spain
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Málaga, Spain
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Gothenburg, Sweden
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Solna, Sweden
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Umeå, Sweden
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Taipei, Taiwan
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Bellshill, United Kingdom
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Birmingham, United Kingdom
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Cardiff, United Kingdom
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Hexham, United Kingdom
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London, United Kingdom
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London, United Kingdom
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Manchester, United Kingdom