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Efficacy and Safety of Enzyme Replacement Therapy in Patients With Fabry Disease
Sponsor: NPO Petrovax
Summary
The goal of this observational study is to learn how enzyme replacement therapy works in patients with Fabry disease. The main question it aims to answer is: What medical problems do participants have? Participants already on enzyme replacement therapy as part of their regular medical care for Fabry disease will be observed as usual. Their data will be collected by their doctor.
Official title: Open-label Comparative Cohort Non-interventional Epidemiological Study of the Efficacy and Safety of Enzyme Replacement Therapy in Russian Patients With Fabry Disease
Key Details
Gender
All
Age Range
8 Years - 65 Years
Study Type
OBSERVATIONAL
Enrollment
100
Start Date
2025-03-24
Completion Date
2027-01
Last Updated
2025-12-31
Healthy Volunteers
No
Conditions
Locations (23)
#13
Astrakhan, Russia
#27
Barnaul, Russia
#7
Borovichi, Russia
#6
Chelyabinsk, Russia
#21
Grozny, Russia
#16
Gubkin, Russia
#26
Irkutsk, Russia
#12
Ivanovo, Russia
#19
Kaa-Khem, Russia
#10
Krasnodar, Russia
#18
Kurgan, Russia
#17
Omsk, Russia
#15
Orenburg, Russia
#9
Perm, Russia
#23
Polevskoy, Russia
#2
Rostov-on-Don, Russia
#4
Rostov-on-Don, Russia
#24
Ryazan, Russia
#8
Saint Petersburg, Russia
#3
Simferopol, Russia
#22
Stavropol, Russia
#11
Ufa, Russia
#5
Voronezh, Russia