Clinical Research Directory

CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain

Sponsor: Fundació Sant Joan de Déu

Summary

The goal of this observational study is to set up a longitudinal data collection study to perform a long-term follow-up of SMA patients in a real-world setting, and to standardise and homogenize the data collection process for SMA patient's data. Treated and untreated patients will be followed based on the routine clinical practice schedule.

Key Details

Conditions

Locations (1)