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RECRUITING
NCT07387367
PHASE3

A Phase 3 Trial to Compare IV BCV Versus IV CDV for Treatment of Adenovirus Infection After Allo-HCT

Sponsor: SymBio Pharmaceuticals

View on ClinicalTrials.gov

Summary

This randomized, open-label, parallel group, two-arm, multi-center assessment will compare IV BCV with IV CDV in adult and pediatric allogeneic HCT recipients with AdV viremia. A virologic response-driven approach to duration of treatment will be evaluated, in which randomized subjects are treated with either BCV or CDV until AdV viremia is confirmed as undetectable or until a maximum of 12 weeks of therapy, whichever occurs first. All subjects will be followed for a total of 24 weeks post-randomization, regardless of treatment assignment. Subjects will be assessed on a weekly basis through the end of treatment visit (EOT). Additional assessments will be performed at the test of cure (TOC) visit, which is 4 weeks after the last dose of study drug and at Weeks 12 and 24 post W1D1.

Official title: A Phase 3, Multicenter, Prospective, Randomized, Open-label Efficacy and Safety Study of Intravenous Brincidofovir Versus Intravenous Cidofovir for Treatment of Adenovirus Infection in Pediatric and Adult Subjects After Allogeneic Hematopoietic Cell Transplantation (Allo-HCT)

Key Details

Gender

All

Age Range

2 Months - Any

Study Type

INTERVENTIONAL

Enrollment

180

Start Date

2026-02-15

Completion Date

2028-06-30

Last Updated

2026-03-13

Healthy Volunteers

No

Interventions

DRUG

cidofovir

CDV does not have a labeled indication for treating Adenovirus infection. CDV will be administered according to local guidelines and institutional standard of care practice.

DRUG

Brincidofovir

Intravenous

Locations (61)

Phoenix Children's Hospital

Phoenix, Arizona, United States

City of Hope

Duarte, California, United States

University of California Davis

Sacramento, California, United States

Rady Children's Hospital

San Diego, California, United States

Children's Hospital Colorado-Center for Cancer and Blood Disorders

Aurora, Colorado, United States

Children's National Hospital

Washington D.C., District of Columbia, United States

Children's Healthcare of Atlanta/Emory

Atlanta, Georgia, United States

Ann and Robert H Lure Children's Hospital

Chicago, Illinois, United States

University of Chicago

Chicago, Illinois, United States

Dana-Farber Cancer Institute-Brighman and Women's

Boston, Massachusetts, United States

Dana-Farber/Boston Children's Cancer and Blood Disorders Center

Boston, Massachusetts, United States

Helen Devos Children's Hospital / Michigan State University

Grand Rapids, Michigan, United States

University of Minnesota

Minneapolis, Minnesota, United States

St Louis Children's Hospital - Barnes Jewish Hospital

St Louis, Missouri, United States

University of Nebraska

Omaha, Nebraska, United States

Joseph M Sanzari Children's Hospital

Hackensack, New Jersey, United States

Cohen Children's Medical Center

New Hyde Park, New York, United States

Weill Cornell Medicine

New York, New York, United States

Duke University Medical Center

Durham, North Carolina, United States

Cincinnati Children's Hospital

Cincinnati, Ohio, United States

Nationwide Children's Hospital

Columbus, Ohio, United States

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

University of Pittsburg Medical Center Children's Hospital

Pittsburgh, Pennsylvania, United States

St. Jude Children's Research Hospital

Memphis, Tennessee, United States

Seattle Children's Hospital

Seattle, Washington, United States

Fred Hutchinson Cancer Center

Seattle, Washington, United States

St. Anna Kinderspital- Childrens Hospital

Vienna, Austria

Leuven, University Hospital Gasthuisberg

Leuven, Belgium

Alberta Children's Hospital University of Calgary

Calgary, Canada

CHU Sainte Justine Hospital

Montreal, Canada

The Hospital for Sick Children

Toronto, Canada

Hôpital Saint-Louis

Paris, France

Necker Hospital

Paris, France

Robert-Debré Hospital, APHP Nord Université de Paris Cité.

Paris, France

Charité University Hospital

Berlin, Germany

Essen University Hospital

Essen, Germany

University Hospital Frankfurt, am Main

Frankfurt, Germany

University Medical Center Hamburg-Eppendorf (UKE)

Hamburg, Germany

Medizinische Hochschule Hannover

Hanover, Germany

University Children's Hospital

Münster, Germany

Kinderheilkunde I | Universitätsklinikum Tübingen

Tübingen, Germany

Istituto Giannina Gaslini

Genova, Italy

Fondazione IRCCS Policlinico San Matteo

Pavia, Italy

Perugia Hospital

Perugia, Italy

Ospedale Pediatrico Bambino Gesu'

Rome, Italy

IRCCS San Raffaele Hospital

San Raffaele, Italy

Leiden Unviversity Medical Center

Leiden, Netherlands

Princess Maxima Center & UMC Utrecht

Utrecht, Netherlands

Instituto Português de Oncologia do Porto (IPO Porto) Francisco Gentil, EPE

Porto, Portugal

Vall d'Hebron University Hospital

Barcelona, Spain

Hospital Universitario La Paz

Madrid, Spain

Clinica Universidad de Navarra

Pamplona, Spain

Karolinska University Hospital

Stockholm, Sweden

Birmingham Women's and Children's Hospital

Birmingham, United Kingdom

Leeds Teaching Hospitals NHS Trust

Leeds, United Kingdom

Great Ormond Street Hospital for Children

London, United Kingdom

University College London Hospitals NHS Foundation Trust

London, United Kingdom

Royal Manchester Children's Hospital

Manchester, United Kingdom

The Newcastle upon Tyne Hospitals NHS Foundation Trust - Freeman Hospital

Newcastle upon Tyne, United Kingdom

Sheffield Children's Hospital

Sheffield, United Kingdom

Royal Marsden Hospital

Sutton, United Kingdom