Clinical Research Directory
Browse clinical research sites, groups, and studies.
Back to Studies
RECRUITING
NCT07834320
Pompe Disease RWE Long-term Monitoring Program
Sponsor: National Taiwan University Hospital
View on ClinicalTrials.gov
Summary
Evaluate short- and long-term biomarker, motor function, respiratory function and safety with avalglucosidase alfa in IOPD and LOPD patients who switched from other ERT.
Official title: Long Term Follow-up for Patients With Pompe Disease Undergoing Compassionate Use and Transitioning to Medication Listed Under the National Health Insurance.
Key Details
Gender
All
Age Range
Any - Any
Study Type
OBSERVATIONAL
Enrollment
40
Start Date
2023-10-01
Completion Date
2036-10-01
Last Updated
2026-09-22
Healthy Volunteers
No
Conditions
Locations (1)
National Taiwan University Hospital
Taipei, Taiwan, Taiwan