Clinical Research Directory

Follow-up of Pediatric Patients Affected by Primary Hyperoxaluria Type 1 (PH1) Treated With Lumasiran

Sponsor: Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico

Summary

The primary objective of the study is to confirm, in pediatric patients with type 1 hyperoxaluria treated with Lumasiran, the reduction in urinary oxalate excretion and plasma oxalate levels-already described at six months-on a larger number of patients and with an extended follow-up (1-5 years), and to evaluate in the same patients the ultrasound-detected reduction in the number of kidney stones over time from the initiation of treatment.

Official title: FOLLOW UP DI PAZIENTI PEDIATRICI AFFETTI DA IPEROSSALURIA DI TIPO 1 IN TRATTAMENTO CON LUMASIRAN

Key Details

Conditions

Locations (1)