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Inherited Retinal Diseases Caused by RPE65 Mutations

Tundra lists 1 Inherited Retinal Diseases Caused by RPE65 Mutations clinical trial. Each listing includes eligibility criteria, study locations, and direct links to research sites in the Tundra directory.

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RECRUITING

NCT05906953

Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)

The purpose of the study is to determine whether HG004 as gene therapy is safe and effective for the treatment of Leber Congenital Amaurosis caused by mutations in RPE65 gene.

Gender: All

Ages: 6 Years - 50 Years

Updated: 2024-09-19

3 states

Leber Congenital Amaurosis

Inherited Retinal Diseases Caused by RPE65 Mutations