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4 clinical studies listed.
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Tundra lists 4 Myotonic Disorders clinical trials. Each listing includes eligibility criteria, study locations, and direct links to research sites in the Tundra directory.
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NCT07008469
Global Open-Label Extension Study of Del-desiran for the Treatment of DM1
A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous Delpacibart Etedesiran (abbreviated del-desiran, formerly AOC 1001) for the Treatment of Myotonic Dystrophy Type 1
Gender: All
Ages: 16 Years - Any
Updated: 2026-02-03
16 states
NCT06411288
Global Study of Del-desiran for the Treatment of DM1
A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Global Study to Evaluate the Efficacy and Safety of Intravenous Delpacibart Etedesiran (abbreviated del-desiran, formerly AOC 1001) for the Treatment of Myotonic Dystrophy Type 1
Gender: All
Ages: 16 Years - 65 Years
Updated: 2026-01-22
18 states
NCT07154654
Prospective, Long Term, Observational Study (Patient Registry) of Paediatric Myotonic Disorders
This is a prospective, open-label, multi-centre, single arm, registry study to collect standard relevant clinical and epidemiological data during routine medical evaluation and treatment in paediatric patients with myotonic disorders who are being treated with mexiletine therapy according to the physician.
Gender: All
Ages: Any - 6 Years
Updated: 2025-09-23
NCT04622553
Open-label Extension Study in Paediatric Patients Who Have Completed the MEX-NM-301 Study.
Open-label Extension Study to Evaluate the Long-term Safety and Efficacy of Mexiletine in Paediatric Patients with Myotonic Disorders Who Have Completed the MEX-NM-301 study.
Gender: All
Ages: 6 Years - 18 Years
Updated: 2025-07-25