Clinical Research Directory
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2 clinical studies listed.
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Tundra lists 2 Ornithine Transcarbamylase (OTC) Deficiency clinical trials. Each listing includes eligibility criteria, study locations, and direct links to research sites in the Tundra directory.
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NCT07773246
Phase 1/2 Study of KRRO-121 in Healthy Volunteers and Patients With UCD
Phase 1/2 Study of KRRO-121 is a randomized, placebo-controlled study in Healthy Volunteers (Phase 1 SAD and MAD) and Study Participants with Urea Cycle Disorders (Phase 2). The primary objective of the study is to evaluate the safety of KRRO-121.
Gender: All
Ages: 18 Years - 65 Years
Updated: 2026-08-19
1 state
NCT03636438
Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency
Determine the long-term safety of DTX301 following a single intravenous (IV) dose in adults with late-onset ornithine transcarbamylase (OTC) deficiency.
Gender: All
Ages: 18 Years - Any
Updated: 2026-06-01
8 states