Clinical Research Directory
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2 clinical studies listed.
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Tundra lists 2 GM1 Gangliosidoses clinical trials. Each listing includes eligibility criteria, study locations, and direct links to research sites in the Tundra directory.
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NCT07479953
A Phase I Study of Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis
This is a study for the administration of in utero AAV9 transfer in prenatally diagnosed Type I or Type II GM1.
Gender: All
Updated: 2026-03-18
NCT03333200
Longitudinal Study of Neurodegenerative Disorders
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions.
Gender: All
Updated: 2026-02-09
1 state